Table 1.
The size of the elements of the expression cassette used to produce the dual hybrid AAVs.
Vector name | Expression cassette elements | Sequence size (bp) |
---|---|---|
AAV-5′ VWF | AAV2 5′ + 3′ ITRs | 260 |
ICAM2 promoter | 336 | |
5′ VWF coding sequence | 4059 | |
Splicing donor site (SD) | 82 | |
AK homology region | 77 | |
AAV-3′ VWF | AAV2 5′ + 3′ ITRs | 260 |
AK homology region | 77 | |
Splicing acceptor site (SA) | 51 | |
3′ VWF coding sequence | 4383 | |
Minimal polyadenylation signal (pA) | 48 |