ADA	adenosine deaminase CRISPR/Cas9: clustered regularly interspaced short palindromic repeats/CRISPR-associated protein 9
ZFNs	zinc finger nucleases
TALEN	transcription activation-like effector nuclease
CAR-T	chimeric antigen receptor– T
AAVs	adeno-associated viruses
Ads	adenoviruses
LVs	lentiviruses
SMA	spinal muscular atrophy
SMN1	survival motor neuron 1
aHUS	atypical hemolytic uremic syndrome
Kb	kilobases
FGFR-1	fibroblast growth factor receptor 1
c-Met	hepatocyte growth factor receptor
ITR	inverted terminal repeat
AAV2	AAV serotype 2
Nabs	neutralizing antibodies
dsDNA	double-stranded DNA
CAR	coxsackie and adenovirus receptor
DSG-2	desmoglein-2
CAV-2	canine adenovirus type 2
OVs	oncolytic viruses
HAd2	human adenovirus serotypes 2
CRAds	conditionally replicating adenoviruses
ICPs	immune checkpoints
CTLA-4	cytotoxic T-lymphocyte-associated protein 4
PD1	programmed cell death 1
PD-L1	programmed cell death ligand 1
NSCLC	non-small-cell lung cancer
RCC	renal cell carcinoma
BAd3	bovine Ad serotype 3
PAd3	porcine Ad serotype 3
HAd	human Ad
Ad5	adenovirus serotype 5
LTR	long terminal repeat
cPPT/CTS	central polypurine tract/chain termination sequence
RRE	Rev responsive element
VSV-G	vesicular stomatitis virus G protein
B-ALL	B-cell acute lymphoblastic leukemia
TDT	transfusion-dependent β-thalassemia
HSC	hematopoietic stem cell
HLA	human leukocyte antigen
NILVs	non-integrating LVs
ATMPs	advanced therapy medicinal products
HSV	herpes simplex virus
BCG	bacillus calmette-guérin
NMIBC	non-muscle invasive bladder cancer
CIS	carcinoma in situ
LBCL	large B-cell lymphoma
CALD	active cerebral adrenoleukodystrophy
MCL	mantle cell lymphoma
RBC	red blood cell
MLD	metachromatic leukodystrophy
ADA-SCID	severe combined immunodeficiency due to adenosine deaminase deficiency
AADC	aromatic L-amino acid decarboxylase
HSCT	hematopoietic stem cell transplantation