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. 2023 May 22:1–18. Online ahead of print. doi: 10.1007/s00011-023-01744-w

Table 2.

Name, company, of some irreversible and reversible BTK inhibitors commercially disposable or under pre-clinical or clinical investigation

Irreversible or Reversible BTKIs Drug Company (Trade name) Clinical indication or pre-clinical trial investigation Clinical Trials.gov number or FDA approved
Irreversible Ibrutinib (Imbruvica®)

(i) Chronic lymphocytic leukemia (CLL), small lymphocytic lymphoma (SLL), Waldenström’s macroglobulinemia (WM), marginal zone lymphoma (MZL), and relapsed/refractory mantle cell lymphoma (MCL);

(ii) Chronic graft-versus-host disease (cGVHD);

(iii) COVID-19 treatment hospitalized patients;

(iv) Refractory/relapsed autoimmune hemolytic anemia;

(v) Anaphylaxis (food allergy);

(vi) Aggressive systemic mastocytosis or mast cell leukemia

(i) FDA approved in 2013; (ii) FDA approved in 2017;

(iii) NCT04375397;

(iv) NCT 04398459 and NTC 03827603;

(v) NCT03149315;

(vi) NCT 02415608

Irreversible Acalabrutinib (Calquence®)

(i) CLL, SLL, MCL;

(ii) COVID-19 treatment hospitalized patients;

(iii) Chronic graft-versus-host disease (cGVHD);

(iv) Anti-MAG neuropathy mediated neuropathy;

(v) Rheumatoid arthritis

(i) FDA approved in 2017;

(ii) NCT04497948 (study prematurely terminated), NCT04380688, NCT04346199;

(iii) NCT04198922;

(iv) NCT05065554;

(v) NCT02387762

Irreversible Zanubrutinib (Brukinsa®)

(i) MCL;

(ii) COVID-19 treatment hospitalized patients

(i) FDA approved in 2019;

(ii) NCT04382586;

Irreversible Tirabrutinib (Velexbru®)

(i) CNS lymphoma, WM, CLL;

(ii) Sjogren Syndrome;

(iii) Rheumatoid arthritis

(i) Approved in Japan;

(ii) NCT03100942;

(iii) NCT02626026;

Irreversible Orelabrutinib (?®)

(i) Relapsed or refractory MCL;

(ii) Phase I study for neuromyelitis optica spectrum disorder

(iii) Phase 2 study for immune thrombocytopenia (ITP)

(iv) Phase 2 study for relapsing–remitting Multiple Sclerosis

(i) FDA approved in 2021 (for MCL);

(ii) NCT05284175;

(iii) NCT05020288;

(iv) NCT04711148

Irreversible Evobrutinib Merk® (i) Relapsing–remitting multiple sclerosis (i) NCT04032171 (terminated) and NCT04338061 (ongoing)
Irreversible Spebrutinib Avila Therapeutics/Calgene® Pre-clinical studies
Irreversible Remibrutinib Novartis®

(i) Phase III for Chronic spontaneous urticaria;

(ii) Allergy to Peanuts;

(iii) Relapsing multiple sclerosis

(i) Expanded access study NCT05170724;

(ii) NCT05432388;

(iii) NCT05147220

Irreversible Tolebrutinib Sanofi®/Principia Biopharma®

(i) Multiple sclerosis;

(ii) Myasthenia gravis

(i) NCT04742400;

(ii) NCT05132569

Irreversible Olmutinib Hamni Pharmaceuticals® Non-small cell lung cancer

NCT04510415 (terminated), NCT03228277,

NCT02722161, NCT02444816,

NCT01894399,

NCT01588145,

NCT02485652 (terminated)

Irreversible Branebrutinib

Bristol-Myers

Squibb®

(i) Atopic dermatitis;

(ii) Rheumatoid arthritis, systemic lupus erythematosus, and primary Sjögren syndrome

(i) NCT05014438 (recruiting);

(ii) NCT04186871 (recruiting)

Irreversible TAK-020 Takeda® Healthy volunteers NTC02723201 and NCT02413255 (both completed)
Irreversible Elsubrutinib AbbVie® Moderately to severely active systemic lupus erythematosus NCT03978520
Irreversible Rilzabrutinib Sanofi®

(i) Chronic spontaneous urticaria;

(ii) IgG4-related disease;

(iii) Warm autoimmune hemolytic anemia wAIHA);

(iv) Healthy volunteers

(v) Atopic dermatitis;

(vi) Immune thrombocytopenia;

(vii) Asthma;

(viii) Pemphigus

(i) NCT05107115 (recruiting);

(ii) NCT04520451 (recruiting);

(iii) NCT05002777 (recruiting);

(iv) NCT04748926 (completed);

(v) NCT05018806 (recruiting);

(vi) NCT04562766 (recruiting)

(vii) NCT05104892 (proof of concept study, recruiting);

(viii) NCT03762265 (terminated)

Reversible Vecabrutinib SNSS® Lymphoid cancers NCT03037645 (phase 1b, terminated)
Reversible GNE-431 Genetech® Pre-clinical investigation
Reversible RN-489 Roche® Pre-clinical investigation
Reversible BMS-935177

Bristol-Myers

Squibb®

Pre-clinical investigation
Reversible BMS-986142

Bristol-Myers

Squibb®

(i) Rheumatoid arthritis;

(ii) Sjögren syndrome

(i) NCT02762123 (completed), NCT02456844 (completed);

(ii) NCT02843659 (proof of concept study, terminated)

Reversible GGI-1746 GGI/Genetech® Pre-clinical investigation
Reversible GDC-0834 Gilead/Genetech® Pre-clinical investigation
Reversible G-744 Gilead/Genetech® Pre-clinical investigation
Reversible G-278 Gilead/Genetech® Pre-clinical investigation (abandoned)
Reversible Fenebrutinib Genetech

(i) Relapsing multiple sclerosis;

(ii) Healthy participants;

(iii) Multiple sclerosis, primary progressive;

(iv) Chronic spontaneous urticaria

(i) NCT05119569, NCT04586010, NCT04586023 (all recruiting);

(ii) NCT03596632 (completed)

(iii) NCT04544449 (recruiting);

(iv) NCT03693625 (terminated)

cGVHD chronic graft-versus-host disease, CNS central nervous system, CLL Chronic lymphocytic leucemia, ITP immune thrombocytopenia, MAG myelin-associated, MCL relapsed/refractory mantle cell lymphoma, MZL marginal zone lymphoma, NCT National Clinical Trial, SLL small lymphocytic lymphoma, wAIHA warm autoimmune hemolytic anemia, WM Waldenström’s macroglobulinemia WM