. Author manuscript; available in PMC: 2024 May 1.

Published in final edited form as: Mol Genet Metab. 2023 Apr 15;139(1):107584. doi: 10.1016/j.ymgme.2023.107584

Table 1. Summary statistics for the clinical measures.

ABC: Vineland-3 adaptive behavior composite. CGI: clinician global impression of change. IQR = interquartile range. SD: standard deviation. UBDRS: Unified Batten Disease Rating Scale. VIQ: verbal intelligence quotient.

	n	Mean±SD	Range	Median[IQR]
Age (years)	27	11.0±4.1	6.0–20.7	9.9 [7.6, 14.8]
VIQ	21	74.9±19.2	45–106	70 [59, 93]
Vineland-3 ABC	27	58.6±21.7	20–84	66 [38.5, 78.5]
UBDRS Physical	27	18.0±18.6	2–64	10 [4.5, 21.5]
UBDRS Capability	27	6.9±2.8	1–14	6 [5.5, 9]
UBDRS CGI	27	15.9±5.1	9.3–24.5	16.3 [11.1, 19.8]