| AAV | Adeno-associated viruses |
| ABE | Adenine base editor |
| Ad | Adenoviruses |
| AS | Angelman syndrome |
| BE3 | Base editor 3 |
| Cas9 | CRISPR-associated protein 9 |
| CRISPR | Clustered regularly interspaced short palindromic repeats |
| DOGS | 5-Carboxyspermylglycine dioctadecylamide |
| DOPE | 1,2-Dioleoyl-sn-glycero-3-phosphoethanolamine |
| dsDNA | Double-stranded DNA |
| DSB | Double-strand break |
| E | Embryonic day |
| EGFP | Enhanced green fluorescent protein |
| Eomes | Eomesodermin |
| EP | Electroporation |
| Fah | Fumarylacetoacetate hydrolase |
| FACS | Fluorescence-activated cell sorting |
| GFP | Green fluorescent protein |
| Gria2 | Glutamate ionotropic receptor AMPA type subunit 2 |
| Grin1 | Glutamate ionotropic receptor NMDA type subunit 1 |
| gRNA | Guide RNA |
| HCM | Hypertrophic cardiomyopathy |
| HDR | Homology directed repair |
| HGD | Hydrodynamics-based gene delivery |
| HIV | Human immunodeficiency virus |
| Hpd | Hydroxyphenylpyruvate dioxygenase |
| HT1 | Hereditary tyrosinemia type 1 |
| Idua | α-L-iduronidase |
| KD | Knock-down |
| KI | Knock-in |
| KO | Knockout |
| MHCα | Myosin heavy chain α |
| miRNA | MicroRNA |
| MPS-IH | Mucopolysaccharidosis type I |
| Myh6 | Myosin heavy chain 6 |
| NHEJ | Non-homologous end joining |
| NMDA | N-methyl-D-aspartate |
| NP | Nanoparticle |
| Pcsk9 | Proprotein convertase subtilisin/kexin type 9 |
| PNAs | Peptide nucleic acids |
| PogZ | Pogo transposable element derived with ZNF domain |
| RNAi | RNA interference |
| RNP | Ribonucleoprotein |
| rAAVs | Recombinant adeno-associated viruses |
| SaCas9 | Staphylococcus aureus Cas9 |
| Satb2 | Special AT-rich sequence-binding protein 2 |
| Sftpc | Surfactant protein C |
| ssDNA | Single-stranded DNA |
| Snord115 | Small nucleolar RNA, C/D box 115 |
| snoRNAs | Small nucleolar RNAs |
| Tbr2 | T-box brain protein 2 |
| Tg | Transgenic |
| TPGD | Transplacental gene delivery |
| TPGD-GEF | Transplacental gene delivery to acquire genome-edited fetuses |
| UBE3A | Ubiquitin–protein ligase E3A |
| UBE3A-ATS | UBE3A antisense transcript |
| VE | Visceral endoderm |
| YS | Yolk sac |