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. 2023 May 11;12(2):37. doi: 10.3390/biotech12020037
AAV Adeno-associated viruses
ABE Adenine base editor
Ad Adenoviruses
AS Angelman syndrome
BE3 Base editor 3
Cas9 CRISPR-associated protein 9
CRISPR Clustered regularly interspaced short palindromic repeats
DOGS 5-Carboxyspermylglycine dioctadecylamide
DOPE 1,2-Dioleoyl-sn-glycero-3-phosphoethanolamine
dsDNA Double-stranded DNA
DSB Double-strand break
E Embryonic day
EGFP Enhanced green fluorescent protein
Eomes Eomesodermin
EP Electroporation
Fah Fumarylacetoacetate hydrolase
FACS Fluorescence-activated cell sorting
GFP Green fluorescent protein
Gria2 Glutamate ionotropic receptor AMPA type subunit 2
Grin1 Glutamate ionotropic receptor NMDA type subunit 1
gRNA Guide RNA
HCM Hypertrophic cardiomyopathy
HDR Homology directed repair
HGD Hydrodynamics-based gene delivery
HIV Human immunodeficiency virus
Hpd Hydroxyphenylpyruvate dioxygenase
HT1 Hereditary tyrosinemia type 1
Idua α-L-iduronidase
KD Knock-down
KI Knock-in
KO Knockout
MHCα Myosin heavy chain α
miRNA MicroRNA
MPS-IH Mucopolysaccharidosis type I
Myh6 Myosin heavy chain 6
NHEJ Non-homologous end joining
NMDA N-methyl-D-aspartate
NP Nanoparticle
Pcsk9 Proprotein convertase subtilisin/kexin type 9
PNAs Peptide nucleic acids
PogZ Pogo transposable element derived with ZNF domain
RNAi RNA interference
RNP Ribonucleoprotein
rAAVs Recombinant adeno-associated viruses
SaCas9 Staphylococcus aureus Cas9
Satb2 Special AT-rich sequence-binding protein 2
Sftpc Surfactant protein C
ssDNA Single-stranded DNA
Snord115 Small nucleolar RNA, C/D box 115
snoRNAs Small nucleolar RNAs
Tbr2 T-box brain protein 2
Tg Transgenic
TPGD Transplacental gene delivery
TPGD-GEF Transplacental gene delivery to acquire genome-edited fetuses
UBE3A Ubiquitin–protein ligase E3A
UBE3A-ATS UBE3A antisense transcript
VE Visceral endoderm
YS Yolk sac