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. 2023 May 11;12(10):1363. doi: 10.3390/cells12101363
Cas CRISPR-associated protein
CPVT catecholaminergic polymorphic ventricular tachycardia
CRISPR clustered regularly interspaced short palindromic repeats
dCas endonuclease deficient CRISPR-associated protein
DMD Duchenne’s muscular dystrophy
DSB double-stranded DNA break
gRNA guide RNA
HDR homology-directed repair
iPSC induced pluripotent stem cell
LQTS long QT syndrome
nCas9 nicking CRISPR-associated
NHEJ non-homologous end joining
PAM protospacer adjacent motif