Figure 3.
Delivery modalities for CRISPR-Cas-based transcriptional modulators
Retro/lentiviral, AAV, and plasmid vectors encode both dCas-effector and sgRNA, and whereas lentiviral vectors integrate these expression cassettes into the genome, AAV and plasmid vectors are transcribed episomally. RNA delivery relies on in-vitro-transcribed RNA encoding dCas-effector and synthetic sgRNA delivery. Some dCas-effector proteins can be generated as recombinant protein and precomplexed into an RNP complex using synthetic sgRNAs prior to delivery.