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. 2023 Jul 5;63(2):97. doi: 10.3892/ijo.2023.5545

Table II.

Published clinical trials on adoptive EBV-CTL immunotherapy for NPC.

Author, year Design Treatment Sample size Condition Efficacy Safety (Refs.)
Chua, 2001 Pilot EBV-specific CTLs 4 R/M EBV+ NPC 3 EBV burden decrease; 3 died of PD (9-21 months after EBV-CTLs) No ≥G3 toxicity (90)
Comoli, 2004 Preliminary EBV-specific CTLs 1 Relapsed EBV+ NPC SD Temporary worsening of local tumor symptoms (91)
Straathof, 2005 Phase I EBV-specific CTLs 10 Stage III/IV EBV+ NPC in remission or with R/R history 4 pts with previous remission remain disease-free, DFS: 19-27 months; 6 pts with previous R/R NPC: 2 CR; 1 PR; 1 SD; 2 no response 1 pts: Tumor swelling requiring tracheostomy (92)
Comoli, 2005 Phase I EBV-specific CTLs 10 Stage IV EBV+ NPC 2 PR; 4 SD; 4 PD 2 pts: Inflammatory reaction at tumor sites (93)
Louis, 2010 Phase I/II EBV-specific CTLs 23 R/R EBV+ NPC 5 remain in remission; 3 recurrent disease; 3 CR; 2 CRu; 2 PR; 3 SD; 5 PD 1 pts: Tumor swelling requiring tracheostomyp (94)
Lutzky, 2014 Preliminary EBV-specific CTLs 1 R/M EBV+ NPC PR No ≥G3 toxicity (95)
Eom, 2016 Phase I EBV/LMP2A-specific CD8+ T cells (EBViNT) 4 R/R EBV+ NPC 3 PD at week 4; 1 SD at week 4, but PD at week 8 No ≥G3 toxicity (96)
Louis, 2009 Phase I Anti-CD45 mAb followed by EBV-specific CTLs 8 R/M EBV+ NPC 1 CR; 2 SD; 5 PD 1 pts: Transient lymph node swelling (97)
Secondino, 2012 Phase II Fludarabine-cyclophosphamide followed by EBV-specific CTLs 11 Stage IV, EBV+ NPC 2 PR; 4 SD; 5 PD 4 pts: G3 neutropenia; 2 pts: Tumor swelling (98)
Smith, 2012 Phase I EBV-specific CTLs 14 R/M EBV+ NPC 10 SD; mPFS: 4.5 months; median OS: 17.4 months No ≥G3 toxicity (99)
Smith, 2017 Phase II AdE1-LMPpoly vector-based CTLs 29 9 pts: no or minimal residual NPC (N/MRD) 20 pts: active R/M NPC (ARMD) N/MRD: 6 maintain response; 3 PD; ARMD: 12 SD; 8 PD; All: mPFS: 5.5 months; median OS: 38.1 months 2 pts: G3 lung abscess (100)
Huang, 2017 Phase I/II EBV-specific CTLs 21 R/M EBV+ NPC 1 CR; 2 SD; 18 PD; (mPFS: 2.2 months; median OS: 16.7 months) No ≥G3 toxicity (101)
Chia, 2014 Phase II Gemcitabine-carboplatin followed by EBV-specific CTLs 38 R/M EBV+ NPC 3 CR; 22 PR; 11 SD; 1 PD; 1 NA; (3-year OS 37.1%) No ≥G3 toxicity (102)

NPC, nasopharyngeal carcinoma; EBV, Epstein-Barr virus; CTL, cytotoxic T-lymphocytes; LMP, latent membrane protein; mAb, monoclonal antibody; R/M, recurrent/metastatic; R/R, relapsed/refractory; pts, patients; PD, progressive disease; SD, static disease; CR, complete response; PR, partial response; CRu, unconfirmed complete response; NA, not assessed; DFS, disease-free survival; OS, overall survival; mPFS, median progression-free survival; G3, grade 3.