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. 2023 Aug 9;9(8):e18920. doi: 10.1016/j.heliyon.2023.e18920

Table 5.

Anticonvulsant activity of cenobamate in mice (multiple studies).

Type of Seizure Model Seizure Model (STUDY) Drug, Route & Dose N per dose group ED50 mg/kg (95% CI) TD50 mg/kg (95% CI) Protective Indexa Additional Findings
Chemically induced SC PTZ 85 mg/kg (NINDS) CBM IP 12, 22, 40, 95 mg/kg 8 28.5 (19.6–42.3) 58.0 (39.5–74.1) 2.0 Inhibition
SC PTZ 95.2 mg/kg (F) CBM IP 3, 5, 8, 12 mg/kg 8 3.8 (2.3–6.2) NT NA DD inhibition
ESM IP 70, 80, 90, 100 mg/kg 8 96.2 (77.3–96.1) NT NA DD inhibition
CBM PO 5, 7, 10 mg/kg 8 7.1 (5.3–9.4) NT NA DD inhibition
ESM PO 200, 250, 300 mg/kg 8 210.6 (181–245) NT NA DD inhibition
SC PTZ 85 mg/kg (G) CBM IP 10, 14, 17, 30 mg/kg 8–10 14.8 (12.6–17.5) NT NA DD inhibition
VPA IP 150 mg/kg 8 NA NT NA 2/8 mice protected
SC bicuculline 2.7 mg/kg (NINDS) CBM IP 30, 70 mg/kg 8 >70 (−) 58.0 (39.5–74.1) <0.8 No inhibition
SC bicuculline 3.4 mg/kg (J) CBM IP 10, 20, 30 mg/kg 8 17.3 (10.9–27.8) NT NA DD inhibition
VPM IP 400, 450, 500 mg/kg 8 468.7 (442–497)
SC bicuculline 3.5 mg/kg (K) CBM IP 10, 20, 30, 40, 50 mg/kg 10 35.4 (−) NT NA DD inhibition from 10 to 40 mg/kg
DZP IP 5 mg/kg 7 NA NT NA 7/7 mice protected
SC picrotoxin 2.5 mg/kg (NINDS) CBM IP 25, 30, 35, 70 mg/kg 8 34.5 (25.9–48.8) 58.0 (39.5–74.1) 1.7 Inhibition
SC picrotoxin 4.5 mg/kg (L) CBM IP 10, 20, 30 mg/kg 8 23.2 (14.9–36.2) NT NA DD inhibition
VPA IP 200, 300, 350, 400 mg/kg 8 341 (307–380)
Electrically induced 6 Hz (NINDS) 22 mA CBM IP 5.4, 10, 15, 20 mg/kg 8 11.0 (6.9–15.4) 58.0 (39.5–74.1) 5.3
32 mA CBM IP 10, 17, 21, 25 mg/kg 8–16 17.9 (14.9–21.1) 3.2
44 mA CBM IP 5.4, 10, 20, 25 mg/kg 8 16.5 (11.6–22.6) 3.5
MES (NINDS) CBM IP 6, 8, 15, 23 mg/kg 8 9.8 (7.8–12.9) 58.0 (39.5–74.1) 5.9 Inhibition
MES (A) CBM IP 3, 8, 12, 15 mg/kg 8 4.2 (2.7–6.7) NT NA DD inhibition
PHT IP 1,2, 5 mg/kg 8 2.8 (1.5–5.3) NT NA DD inhibition
CBM PO 2, 4, 7, 10 mg/kg 8 3.3 (2.2–5.0) NT NA DD inhibition
PHT PO 1,2, 5 mg/kg 8 6.8 (4.7–9.6) NT NA DD inhibition
MES (B) IP 3, 5, 7.5, 10 mg/kg 10 7.0 (5.6–8.6) NT NA DD inhibition
VPA IP 275 mg/kg 10 NA NT NA 6/10 mice protected

CBM, cenobamate; CI, confidence interval; DD, dose-dependent; DZP, diazepam; ED50, median effective dose; ESM, ethosuximide; IP, intraperitoneal; MES, maximal electroshock seizures; NA, not applicable/available; NINDS, National Institute of Neurological Disorders and Stroke; NT, not tested; PHT, phenytoin; PO, oral; PTZ, pentylenetetrazol; SC, subcutaneous; TD50, median neurotoxic dose; VPA, valproic acid/valproate.

aProtective index calculation TD50/ED50. TD50 based on rotarod test.