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. 2023 Aug 29;101(9):e966–e977. doi: 10.1212/WNL.0000000000207547

Figure 3. Survival Curves for Walking Ability and Respiratory Function Status for Adult Patients With Pompe Disease in the French Registry.

Figure 3

Time in years from the start of ERT is plotted on the x-axis, whereas the probability of no progression or the proportion of individuals displaying stabilization is shown on the y-axis. The lines are the survival curves. Vertical drops in these curves correspond to events. The number of patients at risk is indicated below. At time 0, the probability of no progression is 1.0 (100% of the patients are in their baseline state). At 5 years, the probability of no progression is approximately 70% for walking ability and 80% for respiratory function status. Median survival is approximately 9.4 years for walking ability and 14.8 years for respiratory function status. ERT = enzyme replacement therapy.