(A) CRISPRa for PAM-flexible dCas9 variants was tested on an mRFP
reporter gene with libraries of alternative 3 nucleotide PAMs at the −81
target site. (B) Reporter gene expression with the dxCas9-NG group (Figure 1A) at NGH, NHG, and NHH PAM
libraries. dxCas9-NG outperforms other variants in every PAM library. (C)
Reporter gene expression with the dSpRY group (Figure 1A) at NRN and NYN PAM libraries. dSpRY exhibited the highest
CRISPRa efficiency. (D) Direct comparisons of reporter gene expression with
dCas9, dxCas9(3.7), dCas9-NG, dxCas9-NG, dSpG, and dSpRY at a representative set
of PAMs. dCas9-NG, dxCas9-NG, and dSpRY performed best at NGN PAMs while dSpRY
outperformed other variants at NAN and NYN PAMs. An scRNA targeting the J306
sequence was used for all library screens and individual PAM assays. To
calculate fold-activation, we used an off-target scRNA (hAAVS1) with an AGG PAM
reporter to define the basal expression level. Basal reporter expression levels
vary <1.5-fold with different dCas9 variants or PAMs (Figure S5). Values in panel D
represent the mean ± standard deviation calculated from n = 3.