Table 1.
Demographic characteristics and anatomical follow-up parameters of Group 1 (management with only WJ-MSCs).
| Patient no | Genetic mutation | Eye | Horizontal EZW | Vertical EZW | FAF field | |||
|---|---|---|---|---|---|---|---|---|
| Time0 | Time1 | Time0 | Time1 | Time0 | Time1 | |||
| 1 | RHO | R | 3.56 | 3.58 | 4.62 | 4.64 | 8.1 | 8.2 |
| 2 | RP1 | L | 3.21 | 3.27 | 3.36 | 3.38 | 7.9 | 8.0 |
| 3 | EYS | R | 1.86 | 1.55 | 1.15 | 0.88 | 3.1 | 2.5 |
| 4 | PCARE | L | 3.93 | 3.39 | 2.72 | 2.02 | 8.2 | 6.6 |
| 5 | RPGR | L | 1.61 | 0.52 | 1.44 | 0.48 | 0.8 | 0.5 |
| 6 | ABCA4 | R | 2.74 | 2.34 | 2.49 | 2.00 | 4.9 | 4.0 |
| 7 | C2ORF | R | 4.01 | 3.88 | 4.02 | 3.88 | 15.1 | 14.0 |
| 8 | USH2A | L | 2.61 | 2.61 | 2.45 | 2.45 | 4.8 | 4.8 |
| 9 | USH2A | L | 3.91 | 3.90 | 3.92 | 3.90 | 14.9 | 14.8 |
| 10 | RP1 | L | 3.90 | 3.47 | 3.86 | 3.43 | 12.2 | 10.4 |
| 11 | PDE6B | R | 3.87 | 3.34 | 3.71 | 3.20 | 9.9 | 8.0 |
| 12 | USH2A | R | 1.02 | 1.02 | 1.09 | 1.09 | 0.8 | 0.8 |
| 13 | PDE6B | L | 1.15 | 0.84 | 1.13 | 0.82 | 1.0 | 0.7 |
| 14 | MERTK | R | 2.23 | 1.88 | 2.08 | 1.65 | 3.8 | 2.4 |
| 15 | PRPF3 | L | 2.18 | 2.18 | 2.14 | 2.14 | 4.1 | 4.1 |
| 16 | RPGR | R | 2.18 | 1.20 | 2.14 | 1.16 | 4.0 | 2.2 |
| 17 | PDE6B | L | 2.90 | 2.30 | 1.32 | 0.81 | 2.8 | 1.6 |
| 18 | TULP1 | L | 1.42 | 1.40 | 1.25 | 1.24 | 1.1 | 1.0 |
| 19 | USH2A | R | 2.11 | 2.12 | 3.03 | 3.04 | 5.6 | 5.6 |
| 20 | PDE6B | R | 1.11 | 0.89 | 1.14 | 0.91 | 1.0 | 0.7 |
| 21 | BBS2 | R | 1.15 | 1.15 | 1.06 | 1.06 | 1.1 | 1.1 |
| 22 | PRPF3 | L | 2.49 | 2.49 | 2.26 | 2.26 | 4.4 | 4.4 |
| 23 | RP1 | R | 2.51 | 2.49 | 2.54 | 2.52 | 5.1 | 5.0 |
| 24 | RHO | L | 3.18 | 3.20 | 3.21 | 3.21 | 8.9 | 8.9 |
| 25 | RHO | L | 3.26 | 3.26 | 3.14 | 3.14 | 9.0 | 9.0 |
| 26 | PRPF3 | L | 2.11 | 2.11 | 2.29 | 2.29 | 4.0 | 4.0 |
| 27 | BBS6 | L | 1.78 | 1.76 | 1.66 | 1.65 | 1.2 | 1.1 |
| 28 | USH2A | R | 1.66 | 1.64 | 1.38 | 1.36 | 1.4 | 1.3 |
| 29 | EYS | R | 1.48 | 1.21 | 1.51 | 1.22 | 1.3 | 0.9 |
| 30 | RHO | L | 4.71 | 4.74 | 4.79 | 4.82 | 15.5 | 15.6 |
| 31 | RHO | R | 4.90 | 4.92 | 3.96 | 3.98 | 15.1 | 16.6 |
| RHO | L | 4.71 | 4.72 | 4.00 | 4.01 | 15.6 | 16.6 | |
| 32 | CERKL | R | 2.57 | 2.28 | 2.44 | 2.15 | 4.1 | 3.2 |
| CERKL | L | 1.98 | 1.76 | 1.87 | 1.64 | 2.9 | 2.1 | |
Time0 (baseline), just before the Wharton Jelly derived mesenchymal stem cell injection.
Time1: 36th month after injection.
Abbreviations: EZW, ellipsoid zone width (mm); FAF, fundus autofluorescence (mm2); WJ-MSCs, Wharton’s jelly derived mesenchymal stem cells.