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. 2023 Oct 3;24(19):14862. doi: 10.3390/ijms241914862
ASO Antisense oligonucleotide
BMD Becker muscular dystrophy
CDS Coding DNA sequence
DMD Duchenne muscular dystrophy
ES Exon skipping
ESE Exonic splicing enhancer
ESS Exonic splicing silencers
FDA Food and Drug Administration
ISE Intronic splicing enhancer
ISS Intronic splicing silencers
NMD Nonsense-Mediated Decay
ONG Oncogene
PTC Premature termination codon
snRNA Small nuclear RNA
TSG Tumor suppressor gene