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. 2023 Oct 2;29(10):2518–2525. doi: 10.1038/s41591-023-02569-0

Table 2.

Primary and secondary endpoints in the intention-to-treat and per-protocol populations

Intention-to-treat population Cloxacillin plus fosfomycin (n = 104) Cloxacillin alone (n = 110) Risk difference % (95% CI) P value*
Primary endpoint
 Treatment success at day 7 83 (79.8%) 82 (74.5%) 5.3 (−5.95–16.48) 0.360
Secondary endpoints
 All-cause mortality at day 7 4 (3.8%) 1 (0.9%) 2.9 (−2.1–7.97) 0.333
 All-cause mortality at end of therapya 10 (9.6%) 14 (12.7%) −3.1 (−11.53–5.31) 0.453
 All-cause mortality at TOCb 10 (9.6%) 17 (15.5%) −5.9 (−14.66–2.98) 0.196
 Persistent bacteremia at day 3c 4/95 (4.2%) 18/102 (17.6%) −13.4 (−22.88–−3.99) 0.006
 Persistent bacteremia at day 7d 2/90 (2.2%) 4/97 (4.1%) −1.9 (−7.97–4.16) 0.748
 Microbiological treatment failure at 14 dayse 0 (%) 0 (%)
 Relapsing bacteremia at TOCf 0/93 (0%) 1/102 (1%) −0.9 (−3.87–1.91) 1
 Complicated bacteremia at TOCg 21/95 (22.1%) 35/105 (33.3%) −11.2 (−23.51–1.06) 0.077
 Emergence of fosfomycin-resistant strains at TOC 0 (0%) 0 (0%)
 Length of intensive care unit stay, median (IQR), days 8.0 (3.0–17.0) 4.0 (3.25–8.50) 0.355
 Duration of intravenous antibiotic treatment, median (IQR), days 14.0 (11.0–22.0) 15.5 (11.0–26.0) 0.245
 Serious adverse events leading to discontinuation of therapyh 11 (10.6%) 9 (8.2%) 2.40 (−5.43–10.22) 0.547
Per-protocol population Cloxacillin plus fosfomycin (n = 101) Cloxacillin alone (n = 106) Risk difference % (95% CI) P value*
Primary endpoint
 Treatment success at day 7 81 (80.2%) 81 (76.4%) 3.8 (−7.43–15) 0.51
Secondary endpoints
 All-cause mortality at day 7 2 (2%) 0 (0%) 2 (−1.7–5.66) 0.145
 All-cause mortality at end of therapya 10 (9.9%) 11 (10.4%) −0.5 (−8.7–7.75) 0.91
 All-cause mortality at TOCb 10 (9.9%) 14 (13.2%) −3.3 (−11.99–5.38) 0.458
 Persistent bacteremia at day 3c 4/94 (4.3%) 17/99 (17.2%) −12.9 (−22.43–−3.4) 0.005
 Persistent bacteremia at day 7d 2/88 (2.3%) 4/95 (4.2%) −1.9 (−8.13–4.26) 0.684
 Microbiological treatment failure at 14 dayse 0 (%) 0 (%)
 Relapsing bacteremia at TOCf 0/91 (0%) 1/99 (1%) −1 (−3.99–1.97) 1
 Complicated bacteremia at TOCg 20/93 (21.5%) 34/102 (33.3%) −11.8 (−24.21–0.56) 0.078
 Emergence of fosfomycin-resistant strains at TOC 0 (0%) 0 (0%)
 Length of intensive care unit stay, median (IQR), days 9.0 (4.75–15.8) 4.0 (3.25–8.50) 0.168
 Duration of intravenous antibiotic treatment, median (IQR), days 14.0 (11.0–22.0) 16.0 (11.0–26.0) 0.181
 Serious adverse events leading to discontinuation of therapyh 10 (9.9%) 6 (5.7%) 4.2 (−4.03–12.51) 0.304

*The P values were obtained from a two-sided test for differences in proportions.

aEnd of therapy visit 48 h after the last dose of antibiotic treatment.

bTOC visit 12 weeks after randomization.

cAt least one positive blood culture for MSSA at day 3.

dAt least one positive blood culture for MSSA at day 7.

eDefined as a positive sterile site culture for MSSA at least 14 days after randomization.

fAt least one positive blood culture for MSSA at least 72 h after a preceding negative culture at TOC.

gDefined as persistent bacteremia, endocarditis, metastatic emboli or the presence of prosthetic devices at TOC.

hDuring the first 7 days after randomization.