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Proposed treatment terms and definitions and potential paths for patient identification and treatment. DMT, disease‐modifying treatment; N, nusinersen; OA, onasemnogene abeparvovec; R, risdiplam; SMA, spinal muscular atrophy. SMN, survival motor neuron. aNusinersen/risdiplam discontinued, or no doses of nusinersen/risdiplam received after onasemnogene abeparvovec infusion.
