Skip to main content
. 2023 Oct 5;7(22):7007–7016. doi: 10.1182/bloodadvances.2023011308

Table 3.

Selected studies of allo-HCT in BPDCN

Publication Study N Remission status at allo-HCT (n) Donor type (n) Regimen intensity (n) Outcomes
Roos-Weil et al14 EBMT 34 CR1 = 19
>CR1 = 15
MSD = 11
MUD = 23
MAC = 25
RIC/NMA = 9
3-y OS: 41%
3-y NRM: 30%
3-y relapse: 32%
Kharfan-Dabaja et al12 North America 37 CR1 = 28
>CR1 = 9
MSD=16
MUD = 12
Other: 9
MAC = 20
RIC/NMA = 17
3-y OS: 58%
1-y NRM: 25%
3-y relapse: 10%
Bashir et al13 MDACC 17 CR1 = 10
>CR1 = 7
MSD = 5
MUD = 5
Other: 7
MAC = 13
RIC/NMA = 4
5-y OS: 40%
1-y NRM: 29%
5-y relapse: 22%
Murthy et al (this study) CIBMTR 164 CR = 121
>CR1 = 43
MSD = 41
MUD = 65
Other = 58
MAC = 84
RIC = 80
5-y OS: 51.2%
5-y NRM: 23.3%
5-y relapse: 32.2%

MDACC, MD Anderson Cancer Center; MSD, matched sibling donor; MUD, matched unrelated donor.

Umbilical cord blood = 4, haploidentical = 3, mismatch unrelated = 2.

Umbilical cord blood = 3, haploidentical = 4.

Umbilical cord blood = 11, haploidentical = 28, mismatch unrelated = 10, multidonor = 1, unknown = 8.