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. 2023 Nov 22;14:1234262. doi: 10.3389/fphar.2023.1234262

TABLE 5.

Mean trough concentration unbound and ALK occupancy at steady state in plasma and CSF in ALK-positive NSCLC patients.

Drug Dosing regimen Therapeutic target ALK occupancy threshold (%) Cetv (ng/mL) Ki(nM) against ALK Unbound Ctrough (nM, 90% CI) Minimal ALK occupancy (%, 90% CI)
Plasma Unbound CSF Plasma Intracranial
CRI 250 mg BID ALK (wild-type) 75 235 10 78.2 (61.9, 94.5) 1.56 (1.24, 1.89) 88.7 (86.1, 90.4) 13.5 (11.0, 15.9)
ALK (L1196M) - 446 14.9 (12.2, 17.5) 0.3 (0.28, 0.42)
ALK (G1269A) - 250 23.8 (19.8, 27.4) 0.6 (0.49, 0.75)
ALK (G1202R) - 191 29.0 (24.5, 33.1) 0.8 (0.65, 0.98)
ALE + M4 600 mg BID ALK (WT) 435 1.0 11.0 (8.8, 13.1) 8.5 (6.8, 10.1) 91.7 (89.8, 94.2) 89.7 (87.2, 91.0)
ALK (L1196M) - 0.8 93.2 (91.7, 80.9) 91.6 (89.5, 92.7)
ALK (G1269A) - 4.0 73.3 (68.8, 76.6) 68.5 (63.0, 71.6)
ALK (G1202R) - 29 27.5 (23.3, 31.1) 23.0 (19.0, 25.8)
LOR 100 mg OD ALK (WT) 7.6 1.0 160 (140, 179) 123 (108, 138) 99.5 (99.5, 99.7) 99.4 (99.3, 99.5)
ALK (L1196M) 62 17 93.8 (93.0, 94.5) 92.1 (91.1, 92.9)
ALK (G1269A) - 5.0 94.9 (94.3, 95.5) 93.5 (92.7, 94.2)
ALK (G1202R) 150 25 83.1 (81.2, 84.6) 79.1 (76.9, 80.9)

-, not reported data; Cetv, effective PK threshold values.