AAV	adeno-associated viral vector
Ad	adamantane-grafted
b/a-ratio	ratio between the b-wave and a-wave amplitudes
Bp	base pair
C	cytosine
CAG	complex consisting of CMV early enhancer (C), chicken beta-actin promoter, first intron and first exon (A), and rabbit beta-globin splice adaptor (G)
CB	chicken beta-actin
CD-PEI	carbon dot- polyethylenimine
CI	confidence interval
CMV	cytomegalovirus
cND	carboxylated nanodiamond
CRISPR	clustered regularly interspaced palindromic repeats
D	days
EGFP	enhanced green fluorescent protein
ENU	N-ethyl-N-nitroso-ureum
ERG	electroretinography
EMA	European medicine agency
Exo-AAV	exosome-associated AAV
FDA	Food and drug administration
GFAP	glial-fibrillary protein
GFP	green fluorescent protein
H	hours
hiPSC	human induced pluripotent stem cell
hRSp4	a complex consisting of the RS1 promoter, human RS1 cDNA with a truncated first intron, human beta-globin polyadenylation site and AAV2 inverted terminal repeats
H&E	haematoxylin and eosin
IHC	immunohistochemistry
ILM	inner limiting membrane
INL	inner nuclear layer
IRBP	interphotoreceptor retinoid-binding protein
IRD	inherited retinal disease
IS	inner segment
IVI	intravitreal injection
Kb	kilobase
KI	knock-in
KO	knock-out
M	months
Mini-mGluR6	a shortened version of the ON bipolar cell-specific promoter mGlu6
miRNA	microRNA
mOP	mouse opsin
MPI	months post-injection
mRNA	messenger ribonucleic acid
N	no
NR	not reported
N/A	not-applicable
OCT	optical coherence tomography
ONL	outer nuclear layer
OS	outer segment
P	postnatal day
PANAM	polyamidoamine
PBS	phosphate buffered saline
pCEP4	vector encompassing the CMV promoter and a hygromycin resistance marker
pCMS	immediate early promoter of CMV
PEG	polyethylene glycol
Ple155	human-DNA MiniPromoter specific to ON bipolar cells
pRS1HR-gRNA	plasmid including a 950-bp RS1 repair template and the gRNA expression cassette
PI	post-injection
PR	photoreceptor
Rho	rhodopsin
RPE	retinal pigment epithelium
RS1	retinoschisin
Rs1h	RS1 homolog in rodents
scRS/IRBP	modified RS1 promoter coupled with an interphotoreceptor retinoid-binding protein
sgRNA	single guide RNA
shH10	Müller-cell specific serotype derived from the AAV6 shuffled library
siRNA	small interfering RNA
SLN	solid lipid nanoparticles
SLO	scanning laser ophthalmoscopy
SMNP	supramolecular nanoparticle
SMD	standardized mean differences
SRI	subretinal injection
T	thymine
TAT	adenosine-5’-rp-alpha-thio-triphosphate
U6	type III RNA polymerase promoter
VA	visual acuity
Vg/eye	vector genomes per eye
W	weeks
WB	Western blot
WT	wildtype
XLRS	X-linked juvenile retinoschisis
ZsGreen	Zoanthus sp. Green
2tYF	AAV2-derived serotype with three tyrosine (Y) residues mutated to phenylalanine (F)