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. Author manuscript; available in PMC: 2024 Jan 30.
Published in final edited form as: Mol Genet Metab. 2022 Aug 2;137(1-2):127–139. doi: 10.1016/j.ymgme.2022.07.017

Fig. 2.

Fig. 2.

Least-squares mean change from baseline in (A) DAS-II scores over 52 weeks and (B) DAS-II composite, cluster, and subtest scores at week 52 in the ITT population (MMRM analysis). aSubtests included in the early years batteries of the DAS-II differ. In total, 46 of the 49 patients included in the trial were assessed with the early years battery; therefore, these results are presented. T-score data for the school age battery are not available owing to the small number of patients (n = 3). CI, confidence interval; DAS-II, Differential Ability Scales-II; GCA, General Conceptual Ability; IT, intrathecal; MMRM, mixed-effects model for repeated measures; SE, standard error; SNC, special non-verbal composite.