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. Author manuscript; available in PMC: 2024 Dec 1.
Published in final edited form as: Br J Haematol. 2023 Aug 16;203(5):774–780. doi: 10.1111/bjh.19037

Table 1:

Patient and CAR T-cell Treatment Characteristics

Patient ID Age at CAR T-cell Therapy, Sex MCL Histology & Ki67 (%) at Diagnosis TP53 Status at Diagnosis Prior Lines of Therapy: Total (CNS-directed) Previous HCT POD24 CNS Disease Location & Symptoms Disease Presence at Time of CAR T-cell Therapy CAR T-cell Product CRS: Max Grade, Duration (days); Treatment ICANs: Max Grade, Duration (days); Treatment

A 48, F Blastoid; 95% IHC: NA FISH: NA NGS: NA 6 (3) Yes, auto Yes LMD & Parenchyma; lower extremity weakness Systemic: No CNS: Yes Brexu-cel - -
B 57, F Blastoid; 50% IHC: NA FISH: NA NGS: mutation absent 3* (0) Yes, allo Yes LMD; none Systemic: Yes CNS: No Brexu-cel Grade 2, 5d; steroids, toci., anakinra Grade 3, 16d; steroids, toci., anakinra
C 51, F NA 26% IHC: NA FISH: NA NGS: mutation present 4 (2) No Yes Parenchyma; pan-hypopituitarism Systemic: No CNS: Yes Brexu-cel Grade 1, 1d; no treatment Grade 1, 8d; no treatment
D 57, M NA IHC: NA FISH: del(17p) present NGS: NA 4* (1) Yes, auto Yes LMD; seizures Systemic: No CNS: Yes Brexu-cel Grade 1, 8d; toci. Grade 3, 3d; dex., anakinra
E 79, M Blastoid; 90% IHC: NA FISH: no del(17p) NGS: mutation absent 4* (0) No Yes LMD & parenchyma; AMS Systemic: Yes CNS: Yes Brexu-cel Grade 3, 8d; steroids, toci. Grade 3, 23d; steroids, toci., IVIG
F 64, M NA IHC: NA FISH: no del(17p) NGS: mutation absent 2* (1) No No Parenchyma; headache, CN palsy Systemic: No CNS: No Brexu-cel Grade 2, 7d; steroids, toci., anakinra -
G 78, M Classic; 10–20% IHC: Positive (80%) FISH: NA NGS: NA 7* (2) No Yes LMD; vision loss Systemic: No CNS: Yes Brexu-cel Grade 2, 6d; dex., toci. Grade 3, 13d; dex., toci., anakinra
H 64, M Pleomorphic; 20% IHC: NA FISH: NA NGS: mutation absent 4* (1) No Yes LMD; headache Systemic: Yes CNS: Yes Brexu-cel Grade 1, 3d; toci. -
I 75, F Pleomorphic; >95% IHC: Positive (>95%) FISH: NA NGS: NA 4* (1) No Yes LMD; double vision (CN III palsy) Systemic: Yes CNS: No Brexu-cel Grade 1, 4d; dex., toci. Grade 3, 10d; dex., toci.
J 44, F Blastoid; 50% IHC: NA FISH: NA NGS: NA 4* (1) No Yes LMD; bilateral CN VII palsies Systemic: Yes CNS: Yes Tisa-cel Grade 1, 2d; dex. Grade 1, 5d; dex.
*

Indicates bridging therapy was received (defined as any therapy from time of apheresis to CAR T-cell infusion). allo, allogeneic; auto, autologous; brexu-cel, brexucabtagene autoleucel; CAR, chimeric antigen receptor; CNS, central nervous system; CRS, cytokine release syndrome; d, days; dex., dexamethasone; F, female; HCT, hematopoietic cell transplantation; ICANS, immune effector cell-associated neurotoxicity syndrome; IHC, immunohistochemistry; IVIG, intravenous immunoglobulin; LMD, leptomeningeal disease; M, male; MCL, mantle cell lymphoma; max, maximum; NA, not available; NGS; next-generation sequencing; POD24, progression of disease within 24 months of diagnosis; tisa-cel, tisagenlecleucel; toci., tocilizumab