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Vector genome biodistribution
Vector genome copies/nucleus at the end of part 1 (12 weeks after initial GTT dosing in the gastrocnemius biopsy) and at the end of part 2 (endpoint of study) in the tibialis anterior, gastrocnemius, heart, diaphragm, and liver in NHPs from cohort 1 (blue), cohorts 2–4 (red), and cohort 5 (green). Bars represent the mean ± SEM. The endpoint was 12 weeks post-dosing GTT in part 2.
