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. 2024 Mar;76(2):251–266. doi: 10.1124/pharmrev.123.000967

TABLE 3.

Examples of potential neurotoxicity biomarkers used in longitudinal studies

Fluid Based - Longitudinal and Minimally Invasive Direct Analysis of Plasma, Serum, Urine, or CSF
Biomarker Endpoint Comments
F2-IsoPs (F2-iso prostanes) Indirect measurement of oxidative injury Used clinically as biomarker of exposure
Not specific for neurotoxicity
Glial fibrillary acidic protein (GFAP) Biomarker of all types of neural (neuronal and glial) damage ELISA already developed
GFAP is a sensitive and specific marker of astrogliosis (indicative of all types of CNS damage)
Microtubule-associated protein (MAP-2) Biomarker of dendritic injury ELISA already developed
Myelin basic protein (MBP) Biomarker of myelin disruption Immunoassay developed but not widely used
Microtubule-associated protein tau (total τ, phosphorylated τ, and cleaved τ) Biomarker of neurodegeneration/axonal injury ELISAs developed
Neurofilament (light chain and phosphorylated heavy chain) Biomarkers of axonal injury ELISA exists
Spectrin breakdown product (SBDP-145) Found in the CSF as a biomarker for neurodegeneration (apoptosis and necrosis) Recently reported
TSPO (translocator protein) Biomarker of activated glia Has been validated in a variety of preclinical models of neurotoxicity including preclinical and clinical imaging
UCH-L1 (ubiquitin C-terminal hydrolase) Biomarker of cell body injury Immunoassay developed
Imaging - Less Invasive Longitudinal Analysis in Living Animals or High-Resolution in Post Mortem Fixed Animals
MRI T2 relaxation Detects edema, hemorrhage, water redistribution, cellular disruption, cellular density, infiltration, blood flow changes, and temperature changes Data obtained using T2 relaxation is quantitative
Correlation to pathology can be achieved via digital analysis
Electroencephalography and in vivo electrophysiology Permits repeated measurements of neural activity and dose-response effects within subject Invasive
Electrical, electrode, muscle, and movement artifact
Magnetic resonance spectroscopy (MRS) Noninvasive
Permits within-subject repeated measurements of brain metabolites associated with toxicity
Positron emission tomography (PET) Minimally invasive in vivo imaging
MicroPET Molecular-level view of biochemical, physiologic, pathologic, and pharmacological processes in vivo Tags for specific neurotransmitter receptor systems can be used
Resolution less specific than MRI needs specific short-lived radiolabeled ligand to probe the function of interest

CFS, cerebrospinal fluid; CNS, central nervous system.