Fig. 5.
Current clinical applications of rAAV in major human diseases. Clinical applications of rAAV across a spectrum of significant human diseases, including ocular, neurological, metabolic, hematological, neuromuscular, cardiovascular diseases, and oncology. Refer to Supplementary Table 1 for a comprehensive list of 238 clinical trials employing rAAV-based gene therapy for the aforementioned diseases. Figure created with Biorender.com