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. 2024 Apr 29;15(2):689–709. doi: 10.21037/jgo-24-218

Table 6. Adverse events with targeted agents in epNEN patients at unadjusted cohort.

Adverse events Surufatinib, n=87, n (%) Everolimus, n=41, n (%) P value (any grade) P value (grade ≥3)
Any grade Grade ≥3 Any grade Grade ≥3
Any AE 73 (83.9) 27 (31.0) 32 (78.0) 7 (17.1) 0.42 0.09
Hypertension 30 (34.5) 14 (16.1) 0 0 <0.001 0.005
Proteinuria 33 (37.9) 2 (2.3) 1 (2.4) 0 <0.001 >0.99
WBC decreased 7 (8.0) 2 (2.3) 4 (9.8) 0 0.74 >0.99
Neutrophil decreased 3 (3.4) 1 (1.1) 3 (7.3) 2 (4.9) 0.38 0.24
Febrile neutropenia 0 0 1 (2.4) 1 (2.4) 0.32 0.32
LYM decreased 12 (13.8) 2 (2.3) 7 (17.1) 0 0.62 >0.99
Anemia 15 (17.2) 3 (3.4) 15 (36.6) 3 (7.3) 0.01 0.38
PLT decreased 6 (6.9) 3 (3.4) 4 (9.8) 0 0.72 0.55
Hemorrhage 6 (6.9) 1 (1.1) 1 (2.4) 0 0.42 >0.99
Occult blood positive 5 (5.7) 0 0 0 0.17 NA
AST increased 16 (18.4) 2 (2.3) 7 (17.1) 1 (2.4) 0.85 >0.99
ALT increased 9 (10.3) 2 (2.3) 4 (9.8) 0 >0.99 >0.99
ALP increased 4 (4.6) 1 (1.1) 5 (12.2) 0 0.14 >0.99
GGT increased 8 (9.2) 3 (3.4) 7 (17.1) 1 (2.4) 0.24 >0.99
LDH increased 18 (20.7) 0 9 (22.0) 0 0.87 NA
Bilirubin increased 17 (19.5) 3 (3.4) 1 (2.4) 0 0.009 0.55
Hypoalbuminemia 12 (13.8) 0 5 (12.2) 0 0.80 NA
Edema 1 (1.1) 0 0 0 >0.99 NA
Creatinine increased 9 (10.3) 0 2 (4.9) 1 (2.4) 0.50 0.32
Hyperuricemia 18 (20.7) 1 (1.1) 1 (2.4) 0 0.007 >0.99
Hyperlipemia 7 (8.0) 0 10 (24.4) 0 0.01 NA
Hyperglycemia 8 (9.2) 0 15 (36.6) 0 <0.001 NA
Hypoglycemia 3 (3.4) 0 0 0 0.55 NA
TSH increased 22 (25.3) 0 0 0 <0.001 NA
Hypothyroidism 3 (3.4) 0 0 0 0.55 NA
Nausea/vomiting 2 (2.3) 0 1 (2.4) 0 >0.99 NA
Diarrhea 13 (14.9) 0 2 (4.9) 0 0.14 NA
Abdominal discomfort 1 (1.1) 0 0 0 >0.99 NA
Stomatitis 0 0 9 (22.0) 1 (2.4) <0.001 0.32
Muscle pain 1 (1.1) 0 0 0 >0.99 NA
Fatigue 6 (6.9) 0 2 (4.9) 0 >0.99 NA
HFS reaction 1 (1.1) 0 2 (4.9) 0 0.24 NA
Cough 0 0 1 (2.4) 0 0.32 NA
Interstitial pneumonia 0 0 4 (9.8) 0 0.009 NA
Infection 1 (1.1) 0 2 (4.9) 0 0.24 NA
Cardiac toxicity 1 (1.1) 0 2 (4.9) 0 0.24 NA

AE, adverse event; epNEN, extrapancreatic neuroendocrine neoplasm; WBC, white blood cell; LYM, lymphocyte; PLT, platelet; AST, aspartate aminotransferase; ALT, alanine aminotransferase; ALP, alkaline phosphatase; GGT, γ-glutamyl transferase; LDH, lactate dehydrogenase; TSH, thyroid-stimulating hormone; HFS, hand-foot skin syndrome; NA, not available.