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. 2023 Jul 6;11(5):101020. doi: 10.1016/j.gendis.2023.04.040

Table 2.

List of some epigenetic drugs in clinical trials.

Targets Drugs/inhibitors Phase Types of cancer/tumor
DNA methyltransferase (DNMT) Guadecitabine (SGI-110) Phase I Cholangiocarcinoma, malignant melanoma, non-small cell lung cancer, pancreatic cancer, mesothelioma
Phase II Acute myeloid leukemia, chronic myelomonocytic leukemia, bladder cancer; myeloproliferative disorders, ovarian cancer
Hydralazine (apresoline) Phase I Solid tumors
Phase II Cutaneous T-cell lymphoma, hepatocellular carcinoma
MG98 (HYB 101584) Phase II Metastatic renal carcinoma
Histone deacetylase (HDAC) VPA (valproic acid) Phase II Glioma, metastatic colorectal cancer
Mocetinostat (MGCD-0103) Phase I Metastatic leiomyosarcoma, pancreatic cancer, melanoma
Phase II Solid tumors;
Resminostat (4SC-201) Phase I Biliary cancer; solid tumors, pancreatic cancer
Phase II Hepatocellular carcinoma, non-small cell lung cancer, Hodgkin lymphoma, biliary cancer
Non-coding RNA MRG-106 Phase I Cutaneous T-cell lymphoma, diffuse large B-cell lymphoma, adult T-cell leukemia/lymphoma, chronic lymphocytic leukemia
MesomiR-1 Phase I Malignant pleural mesothelioma, non-small cell lung cancer
CALAA-01 Phase I Solid tumors
ATU027 Phase I Solid tumors
Phase II Pancreatic cancer
Bromodomain and extra-terminal (BET) Molibresib (I-BET762) Phase I/II NUT carcinoma, solid tumors
Lysine-specific demethylase (LSD) Iadademstat (ORY-1001) Phase I/II Acute myeloid leukemia
GSK2879552 Phase I Small cell lung cancer, acute myeloid leukemia
Disruptor of telomeric silencing 1-like (DOT1L) Pinometostat (EPZ5676) Phase I/II Acute myeloid leukemia