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. 2024 Jul 11;26(11):1964–1980. doi: 10.1093/neuonc/noae131

Table 2.

Responses to Immunotherapy in Syngeneic Brain Tumor Mouse Models

Tumor Model Genetic Background PD1 CTLA4 Others
Gl261 C57BL/6J, carcinogen induced59 Anti-PD1 (yes)90,123–125 Anti-CTLA-4 (no)91,123 anti-CD40 (no)73
Anti-PD1 (yes, minor)86 Anti-CTLA-4 (yes, minor)126 Anti-CD40+ COX-2 inhibitor73(synergistic, minor)
Anti-PD1 (no)127–129 anti-CTLA-4 (yes)130 anti-OX40 (yes)125
Anti-PD1 + anti-CTLA-4 (yes)84,126,131 Anti-CTLA-4 + anti-PDL1(synergistic)130 GVAX (yes, minor)125
Anti-PD1+ anti TIGIT (yes, big)86 Intratumoral IL-12 + anti-CTLA-4 (YES, big)91 IDO inhibitor (no)130
Anti-PD1+ anti TIGIT (yes, mild)127 Anti-PD1 + anti-CTLA4 + CD40131 stimulation (no synergistic) STING antonistic93
Anti-PD1 + TMZ (synergistic)124 Anti-PD1 + anti-CTLA4 + anti-IL6 (synergistic)131 Intratumoral IL-12 (yes, minor)91
Anti-PD1 + focal RT (synergistic)88 Anti-PD1 + anti-CTLA4 + anti-IL6 + CD40 stimulation (overall survival)131 mImp3 peptide vaccine + PolyIC (yes)132
Anti-PD1 + GMCI (synergistic)101 NKG2D CAR-T (yes, mild)133
Anti-PD1 + Zika (synergistic)92 Anti-IL6 + CD40 stimulation (synergistic)131
Anti-PD1 + GVAX (synergistic)125 Anti-IL6 (minor)131
Anti-PD1 + anti-OX40 + GVAX (synergistic, dramatic)125 CD40 stimulation (minor)131
Anti-PD1 + anti-TIM3 + Focal RT87 (overall survival) Anti-TIM3 (no)87
Anti-PD1 + anti-CTLA4 + CD40 stimulation (no synergistic)131 Anti-TIM3 + Focal RT (synergistic)87
anti-PD1 + anti-CTLA4 + anti-IL6 (synergistic)131 Anti-PD1 + anti-TIM3 + focal RT (overall survival)87
Anti-PD1 + anti-CTLA4 + anti-IL6+
CD40 stimulation (overall survival)131
Anti-TIGIT (no)86,127
Anti-PD1 + anti-TIM3 + Focal RT (overall survival)87 Anti-PDL1 (yes)132
Anti-PDL1-LNP/CDK5 inhibitor + RT (synergistic)83
Anti-CTLA-4 + anti-PDL1
(synergistic)130
CT2A C57BL/6J. carcinogen induced58 Anti-PD1 (yes, minor)100–102 Anti-PD1 + anti-CTLA-4 + oncolytic virus delivery of IL12 (synergistic)97 STING antonistic94
Anti-PD1(NO)129 Anti-PD1 + anti-CTLA-4 (no)97 Anti-PDL1 (yes, minor)132
Anti-PD1 + GMCI (synergistic)101 Anti-CTLA-4 (no)102 Neoantigen vaccine + PolyIC + anti-PDL1 (yes, synergistic)132
Anti-PD1 + Zika (synergistic)92 Anti-PDL1 + D2C7 (synergistic)102
Anti-PD1 + anti-CTLA-4+
Oncolytic virus delivery of IL12 (synergistic)97
CT2A C57BL/6J, carcinogen induced Anti-PD1 + anti-CTLA-4(NO)97 Anti-PDL1-LNP/CDK5 inhibitor + RT (synergistic)83
Anti-PD1 + D2C7(synergistic, moderate)102
005GSC FVB/N,C57BL/6, backcross to C57BL/657 Anti-PD1 (no)98 Anti-CTLA-4 (yes, minor)97 Oncolytic virus delivery of IL12 (yes, minor)97
Anti-PD1 (yes, minor)97 Anti-PD1 + anti-CTLA-4 (yes)97 CCR2 antagonist (NO)98
Anti-PD1 + oncolytic virus delivery of IL12 (synergistic)97 Anti-PD1 + anti-CTLA-4 + Oncolytic virus delivery of IL12 (overall long-term survival)97 Anti-PDL1 (yes, minor)97
Anti-PD1 + CCR2 antagonist (yes, modest)98 Anti-CTLA-4 + oncolytic virus delivery of IL12 (synergistic)97 Anti-PDL1 + oncolytic virus delivery of IL12 (synergistic)97
Anti-PD1 + anti-CTLA-4(YES)97
SMA-560 VM/Dk, spontaneous model Anti-PD1 (yes, minor)102 Anti-CTLA-4 (no)91,102 Intratumoral IL-12 (yes, minor)91
Anti-PD1 + D2C7 (immunotoxin)
(synergistic, moderate)102
Anti-CTLA-4 (yes)104 NKG2D CAR-T (yes)133
Anti-CTLA-4 + D2C7 (synergistic, moderate)102 Anti-PDL1 + D2C7(synergistic)102
Intratumoral IL-12 + anti- CTLA-4 (YES, big)91
SB28 C57BL/6, SB GEMM(NRasV12, TP53 shRNA, and mPDGF)73 Anti-PD1 + irradiation (no synergistic)95 Anti-PD1 + anti-CTLA-4 (NO)84 FLT3L (yes, minor)95
Anti-PD1 + anti-CTLA-4 (NO)84 anti-CD40 (no)73
Anti-CD40 + COX-2 inhibitor (synergistic, minor)73
Anti-PDL1 (yes, minor)95
KR158B C57BL/6, 129S4/SvJae, backcross to C57BL/6, NF1 and TP53 KO transgenic mice31 Anti-PD1 (no)90,98 CCR2 antagonist (yes, modest)98
Anti-PD1 + CCR2 antagonist (synergistic)98
GEM tumor cell orthotopic injection Pten–/–, Ink4a-Arf–/–, PDGFb Anti-PD1 + anti-CTLA4 + CD40 stimulation + anti-IL6 (synergistic)131 Anti-PD1 + anti-CTLA4 + CD40 stimulation + anti-IL6 (synergistic)131 Anti-IL6 (minor)131
Anti-PD1 + anti-CTLA4 + anti-IL6 (same as anti-IL6)131 Anti-PD1 + anti-CTLA4 + anti-IL6(same as anti-IL6)131 CD40 stimulation (no)131
Anti-PD1 + anti-CTLA4 (no)131 Anti-PD1 + anti-CTLA4 (no)131
QPP4 FvBXC57BL/6, QPP GEMM (Qki,TP53,PTEN triple ko)109 Anti-PD1 (no)110 Anti-CTLA4 (on)110
QPP5 Anti-PD1 (NO)110 Anti-CTLA4 (YES)110
QPP7 Anti-PD1 (yes)110 Anti-CTLA4 (yes)110
QPP8 Anti-PD1 (no)110 Anti-CTLA4 (no)110