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. 2024 Dec 18;64(1):93–105. doi: 10.1007/s40262-024-01467-z

Table 2.

Characteristics of the 25 patients included in the real-life implementation analysis in terms of adherence, relative forgiveness (RF) and outcomes

All patients
(n = 25)
Group 1
(RF ≥ 0.32)
(n = 19)
Group 2
(RF < 0.32)
(n = 6)
Comparison between the two groups (significance)a
Allopurinol dose (mg)b 300 (100–600) 300 (100–600) 300 (100–600) 1
Adherence data
Total number of missed doses 1237 399 838 < 0.0001
Median number of missed doses per person 33 19 118
Total number of non-implementation eventsd 675 298 377
 Occasional missed doses (n) 108 98 10 < 0.0001
 Repeated missed doses (n) 482 186 296 < 0.0001
 Occasional drug holidays (n) 5 5 0
 Repeated drug holidays (n) 80 9 71 < 0.0001
Proportion of doses taken 91% 95% 67% < 0.0001
Relative forgiveness of implementation patternsb
Relative forgiveness 0.51 (0–1) 0.61 (0.32–1) 0.16 (0–0.26) 0.0003
Outcomesb
Proportion of days at the urate target 75% 86% 41% 0.001
Flares
 Total number 18 10 8 OR = 4.3e [95% CI 0.6–30.6]
 Mean number of flares per person 0.7 0.5 1.3 0.129
HRQoL utility scores 0.9459 0.9456 0.9464 0.838
EQ-VAS scores 80.0 80.0 81.3 0.873

RF = relative forgiveness; OR = odds ratio; CI = confidence interval; occasional missed doses = ≤ 2 consecutive missed doses followed by ≥ 15 consecutive doses taken as prescribed; repeated missed doses = ≤ 2 consecutive missed doses followed by < 15 consecutive doses taken as prescribed; occasional drug holidays = ≥ 3 consecutive missed doses followed by ≥ 15 consecutive doses taken as prescribed; repeated drug holidays = ≥ 3 consecutive missed doses followed by < 15 consecutive doses taken as prescribed; HRQoL = health related quality of life; EQ-VAS = EuroQoL-visual analog scale

ap-value of Mann–Whitney test unless otherwise stated

bMedian (range) unless otherwise specified

cp-value of Fisher’s exact test

dA non-adherence event is any instance of an occasional missed dose, repeated missed dose, repeated missed dose or repeated missed dose throughout the study period

eOdds of having at least one flare in subgroup 2