Skip to main content
. 2025 Mar 20;25:78. doi: 10.1186/s12874-025-02520-6

Table 3.

Results across 1,000 simulated studies for design version a). Average values and interquartile ranges provided

S T1E/ Power Enrolled
patients
ESS %Stop
(1st interim)
%Stop
(2nd interim)
w
(1st interim)
w
(2nd interim)
1 0.044*

1497

(796–1586)

16 (10–18) 33 44

0.47

(0.4–0.56)

0.42

(0.25–0.59)

2 0.8

1850

(1576–2358)

20 (12–28) 13 38

0.45

(0.37–0.56)

0.52

(0.40–0.66)

3 0.048*

1506

(796–1778)

15 (8–19) 34 41

0.4

(0.28–0.52)

0.47

(0.33–0.62)

4 0.83

1835

(1578–2376)

10 (5–15) 15 39

0.36

(0.24–0.49)

0.21

(0.08–0.3)

5 0.05*

1509

(796–2350)

11 (4–15) 35 39

0.32

(0.20–0.44)

0.29

(0.12–0.44)

6 0.85

1829

(1582–2381)

6 (2–9) 14 41

0.29

(0.16–0.41)

0.09

(0.03–0.12)

7 0.04*

1480

(796–1590)

6 (2–7) 35 44

0.20

(0.11–0.26)

0.13

(0.05–0.17)

8 0.88

1792

(1586–2383)

3 (1–4) 15 44

0.19

(0.1–0.25)

0.03

(0.01–0.04)

T1E: Type I Error rate (*); ESS: Effective Sample Size