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. 2025 Mar 20;25:78. doi: 10.1186/s12874-025-02520-6

Table 4.

Results across 1,000 simulated studies for design version b). Average values and interquartile ranges provided

S T1E/ Power Enrolled
patients
ESS %Stop
(1st interim)
%Stop
(2nd interim)
w
(1st interim)
w
(2nd interim)
1 0.052*

1511

(796–1578)

17 (13–26) 32 44

0.5

(0.5–0.5)

0.5

(0.5–0.5)

2 0.8

1846

(1578–2360)

20 (13–26) 13 41

0.5

(0.5–0.5)

0.5

(0.5–0.5)

3 0.052*

1524

(796–2360)

17 (13–26) 34 38

0.5

(0.5–0.5)

0.5

(0.5–0.5)

4 0.83

1806

(1578–2360)

20 (13–26) 14 42

0.5

(0.5–0.5)

0.5

(0.5–0.5)

5 0.061*

1490

(796–1578)

18 (13–26) 35 41

0.5

(0.5–0.5)

0.5

(0.5–0.5)

6 0.87

1821

(1578–2360)

20 (13–26) 12 44

0.5

(0.5–0.5)

0.5

(0.5–0.5)

7 0.055*

1512

(796–2360)

18 (13–26) 34 41

0.5

(0.5–0.5)

0.5

(0.5–0.5)

8 0.87

1784

(1578–2360)

19 (13–26) 15 44

0.5

(0.5–0.5)

0.5

(0.5–0.5)

T1E: Type I Error rate (*); ESS: Effective Sample Size