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. 2025 Jan 4;19(5):101460. doi: 10.1016/j.jcmgh.2025.101460

Table 2.

List of gRNA Oligos for in Vitro and in Vivo Validation

Target gene gRNA Sense In vitro oligo sequence In vivo oligo sequence
Non-targeting sg-NT Fwd caccgGCTCCTGGGGCAGTCACCCA accGCTCCTGGGGCAGTCACCCA
Rev aaacTGGGTGACTGCCCCAGGAGCc aacTGGGTGACTGCCCCAGGAGC
Vps72 sg1-Vps72 Fwd caccgGAACCCTGGTACTGTGCCCT accGAACCCTGGTACTGTGCCCT
Rev aaacAGGGCACAGTACCAGGGTTCc aacAGGGCACAGTACCAGGGTTC
sg2-Vps72 Fwd caccgGCACTCATAGGCAGCGCCTA accGCACTCATAGGCAGCGCCTA
Rev aaacTAGGCGCTGCCTATGAGTGCc aacTAGGCGCTGCCTATGAGTGC
sg3-Vps72 Fwd caccgGCGCCTAGGGCACAGTACCA accGCGCCTAGGGCACAGTACCA
Rev aaacTGGTACTGTGCCCTAGGCGCc aacTGGTACTGTGCCCTAGGCGC
sg4-Vps72 Fwd caccgGGGCTGCTGTGGCCACTCAT accGGGCTGCTGTGGCCACTCAT
Rev aaacATGAGTGGCCACAGCAGCCCc aacATGAGTGGCCACAGCAGCCC
sg5-Vps72 Fwd caccgGTTCACCTTAAGTCTCTTTG accGTTCACCTTAAGTCTCTTTG
Rev aaacCAAAGAGACTTAAGGTGAACc aacCAAAGAGACTTAAGGTGAAC
Zbtb7b sg1-Zbtb7b Fwd caccgGACAGTGTCCGCAGTGGCCA accGACAGTGTCCGCAGTGGCCA
Rev aaacTGGCCACTGCGGACACTGTCc aacTGGCCACTGCGGACACTGTC
sg2-Zbtb7b Fwd caccgGAGGAGGCAAAGGGTGGCGG accGAGGAGGCAAAGGGTGGCGG
Rev aaacCCGCCACCCTTTGCCTCCTCc aacCCGCCACCCTTTGCCTCCTC
sg3-Zbtb7b Fwd caccgGAGGGCTGGACGGGGGTCGG accGAGGGCTGGACGGGGGTCGG
Rev aaacCCGACCCCCGTCCAGCCCTCc aacCCGACCCCCGTCCAGCCCTC
sg4-Zbtb7b Fwd caccgGTGACAGAGGGTGTTGCTAA accGTGACAGAGGGTGTTGCTAA
Rev aaacTTAGCAACACCCTCTGTCACc aacTTAGCAACACCCTCTGTCAC
sg5-Zbtb7b Fwd caccgGTGGAAGCCAGGTGAATGTA accGTGGAAGCCAGGTGAATGTA
Rev aaacTACATTCACCTGGCTTCCACc aacTACATTCACCTGGCTTCCAC
Gba sg1-Gba Fwd caccgGGAATTTTGGGGAGGCCTAA accGGAATTTTGGGGAGGCCTAA
Rev aaacTTAGGCCTCCCCAAAATTCCc aacTTAGGCCTCCCCAAAATTCC
sg2-Gba Fwd caccgGGGCCTCCCCAAAATTCACA accGGGCCTCCCCAAAATTCACA
Rev aaacTGTGAATTTTGGGGAGGCCCc aacTGTGAATTTTGGGGAGGCCC
sg3-Gba Fwd caccgGTAAGCCGGTCACGTGATGC accGTAAGCCGGTCACGTGATGC
Rev aaacGCATCACGTGACCGGCTTACc aacGCATCACGTGACCGGCTTAC
sg4-Gba Fwd caccgGTGAATACAGTGGCCCTCAC accGTGAATACAGTGGCCCTCAC
Rev aaacGTGAGGGCCACTGTATTCACc aacGTGAGGGCCACTGTATTCAC
sg5-Gba Fwd caccgGTGTATGGACAGCTGAGTAG accGTGTATGGACAGCTGAGTAG
Rev aaacCTACTCAGCTGTCCATACACc aacCTACTCAGCTGTCCATACAC
Mrpl9 sg1-Mrpl9 Fwd caccgGCTCTCCGCTGTCCTATCGT accGCTCTCCGCTGTCCTATCGT
Rev aaacACGATAGGACAGCGGAGAGCc aacACGATAGGACAGCGGAGAGC
sg2-Mrpl9 Fwd caccgGGCCTGAGTGGTATAGATAT accGGCCTGAGTGGTATAGATAT
Rev aaacATATCTATACCACTCAGGCCc aacATATCTATACCACTCAGGC
sg3-Mrpl9 Fwd caccgGGGCGTGCAAGGCGGGGTTG accGGGCGTGCAAGGCGGGGTTG
Rev aaacCAACCCCGCCTTGCACGCCCc aacCAACCCCGCCTTGCACGCCC
sg4-Mrpl9 Fwd caccgGTGCCCGCGGCGCGCCTGAG accGTGCCCGCGGCGCGCCTGAG
Rev aaacCTCAGGCGCGCCGCGGGCACc aacCTCAGGCGCGCCGCGGGCAC
sg5-Mrpl9 Fwd caccgGTTAAAAAAAGAGGCGGAGG accGTTAAAAAAAGAGGCGGAGG
Rev aaacCCTCCGCCTCTTTTTTTAACc aacCCTCCGCCTCTTTTTTTAAC