AMA	African Medicines Agency
AdV	Adenoviral
AVAREF	African Vaccine Regulatory Forum
AAV	Adeno-associated viral
CAR T cell	Chimeric antigen receptor T cell
CGD	Chronic granulomatous disease
CRISPR	Clustered regularly interspaced short palindromic repeats
EMA	European Medicine Agency
GMP	Good manufacturing practice
HICs	High-income countries
HSCs	Hematopoietic stem cells
HSPC	Hematopoietic stem and progenitor
LMICs	Low-and middle-income countries
ML3	Maturity Level 3
IV	Intravenous injection
LNPs	Lipid nanoparticles
LMICs	Low-and middle-income countries
SCD	Sickle cell disease
SMA	Spinal muscular atrophy
U.S. FDA	United States Food and Drug Administration
VLPs	Viral-like particles
WHO	World Health Organization