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. 2025 May 13;13:73. doi: 10.1186/s40364-025-00786-y

Table 4.

Clinical trials of Menin inhibitors

Agent Disease Phase Enrollment NCT.gov identifier Status
Revumenib (SNDX-5613)
Revumenib with Azacitidine + Venetoclax Patients with NPM1-mutated or KMT2A-rearranged AML Phase 3 415 NCT06652438 Not yet recruiting
Revumenib Patients with KMT2A-Rearranged or NPM1-Mutated Acute Leukemia After AHSCT Phase 1 27 NCT06575296 Not yet recruiting
Revumenib With 7 + 3 + Midostaurin AML Phase 1 22 NCT06313437 Not yet recruiting
Revumenib and Venetoclax AML MRD positive Phase 2 8 NCT06284486 Recruiting
Revumenib Leukemia Associated with Upregulation of HOX Genes Phase 2 15 NCT06229912 Recruiting
Revumenib and Gilteritinib R/R FLT3-Mutated AML and Concurrent MLL-Rearrangement or NPM1 Mutation Phase 1 30 NCT06222580 Recruiting
Revumenib, Azacitidine, and Venetoclax in Pediatric and Young Adult Patients With R/R AML Phase 1 24 NCT06177067 Recruiting
Revumenib + Daunorubicin and Cytarabine Newly Diagnosed AML Patients with Changes in NPM1 or MLL/​KMT2A Gene Phase 1 28 NCT05886049 Recruiting
Revumenib in Combination with Chemotherapy Patients Diagnosed with R/R Leukemia Phase 2 78 NCT05761171 Recruiting
Radiolabeled Revumenib Adults with Acute Leukemia Phase 1 8 NCT05406817 Recruiting
Revumenib in Combination with Chemotherapy Participants With R/R Acute Leukemia Phase 1 30 NCT05326516 Completed
Revumenib R/R Leukemias Including Those with an MLL/KMT2A Gene Rearrangement or NPM1 Mutation Phase 1/2 413

NCT04065399

(AUGMENT-101)

Recruiting
Ziftomenib (KO-539)
Ziftomenib With Venetoclax and Gemtuzumab Pediatric Patients With AML Phase 1 22 NCT06448013 Not yet recruiting
Ziftomenib Maintenance Post Allo-HCT in AML with NPM1m and KMT2A-r Phase 1 22 NCT06440135 Recruiting
Ziftomenib, Venetoclax and Azacitidine in Pediatric R/R Acute Leukemias Phase 1 22 NCT06397027 Not yet recruiting
Ziftomenib in Combination with Chemotherapy Children with R/R Acute Leukemia Phase 1 20 NCT06376162 Not yet recruiting
Safety and Tolerability of Ziftomenib Combinations KMT2A-r or NPM1-m R/R AML Phase 1 171 e NCT06001788 Recruiting
Ziftomenib with Venetoclax/​Azacitidine, Venetoclax, or 7 + 3 Patients with AML Phase 1 212 NCT05735184 Recruiting
Ziftomenib Patients With R/R AML Phase 1/2 199 NCT04067336 Recruiting
DSP-5336
DSP-5336 R/R AML/ ALL with or Without KMT2A-r or NPM1-m Phase 1/2 70 NCT04988555 Recruiting
DS-1594b
DS-1594bWith or Without Azacitidine, Venetoclax, or Mini-HCVD R/R AML or ALL Phase 1/2 17 NCT04752163 Completed
Bleximenib (JNJ-75276617)
Bleximenib in Combination with Conventional Chemotherapy Pediatric and Young Adult Participants with Relapsed/Refractory Acute Leukemias Phase 1 0 NCT05521087 Withdrawn
Bleximenib in Combination with Directed Therapies Patients with AML Phase 1 200 NCT05453903 Recruiting
Bleximenib patients With Acute Leukemia Phase 1/2 400 NCT04811560 Recruiting
BMF-219
BMF-219 Adult Patients With AML, ALL (With KMT2A/MLL1r, NPM1 Mutations), DLBCL, MM, and CLL/SLL Phase 1 177 NCT05153330 Recruiting
BN104
BN104 Acute Leukemia Phase 1/2 90 NCT06052813 Recruiting