| AAVs | Adeno-associated viruses |
| AD | Alzheimer’s disease |
| ASO | Antisense oligonucleotide |
| BBB | Blood–brain barrier |
| BMSCs | Bone marrow-derived mesenchymal stem cells |
| BPD | Bronchopulmonary dysplasia |
| CSF | Cerebrospinal fluid |
| CNS | Central nervous system |
| DPSCs | Deciduous dental pulp stem cells |
| EVs | Extracellular vesicles |
| FUSIN | Focused ultrasound-mediated nasal drug delivery |
| GLP-1 | Glucagon-like peptide-1 |
| IGF-1 | Insulin-like growth factor 1 |
| hNSCs | Human neural stem cells |
| LIF | Leukemia inhibitory factor |
| MSC | Mesenchymal stem cell |
| NGF | Nerve growth factor |
| OMPCs | Olfactory mucosal progenitor cells |
| PD | Parkinson’s disease |
| PEG | Polyethylene glycol |
| PTD | Protein transduction domain |
| SAD | Social anxiety disorder |
| SCI | Spinal cord injury |
| TBI | Traumatic brain injury |
| ZO-1 | Zonula occludens-1 |