Skip to main content
. 2025 Jun 28;15(7):940. doi: 10.3390/biom15070940
BRB Blood–Retinal Barrier
AAV Adeno-Associated Virus
ssDNA Single-Stranded DNA
wtAAV Wild-Type Adeno-Associated Virus
AAP Assembly Associated Protein
MAAP Membrane-Associated Accessory Protein
rAAV Recombinant Adeno-Associated Virus
ITRs Inverted Terminal Repeats
HSPG Heparan Sulfate Proteoglycan
AAVR Adeno-Associated Virus Receptor
CLIC/GEEC CLathrin-Independent Carrier/GPI-Enriched Endocytic Compartment pathway
SR Injection Subretinal Injection
PRs Photoreceptors
RPE Retinal Pigment Epithelium
IRDs Inherited Retinal Diseases
BSS Balanced Salt Solution
MI-OCT Multimodal Imaging-Optical Coherence Tomography
DR Diabetic Retinopathy
DME Diabetic Macular Edema
RGCs Retinal Ganglion Cells
ILM Internal Limiting Membrane
nAMD Neovascular Age-Related Macular Degeneration
XLRP X-Linked Retinitis Pigmentosa
GTAU Gene Therapy-Associated Uveitis
TLR Toll-Like Receptor
SCI Suprachoroidal Injection
LCA Leber Congenital Amaurosis
BCVA Best Corrected Visual Acuity
RP Retinitis Pigmentosa
DSBs Double-Strand Breaks
HDR Homology-Directed Repair
NHEJ Non-Homologous End Joining
BE Base Editing
PE Prime Editing
NHPs Non-Human Primates
LLVA Low Luminance Visual Acuity
ecDHFR Escherichia coli Dihydrofolate Reductase
NPDR Non-Proliferative Diabetic Retinopathy
PDR Proliferative Diabetic Retinopathy
DRSS Diabetic Retinopathy Severity Scale
AMD Age-Related Macular Degeneration
dAMD Dry Age-Related Macular Degeneration
CNV Choroidal Neovascularization
GA Geographic Atrophy