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. 2025 Jul 23;26(15):7089. doi: 10.3390/ijms26157089
Abbreviation Meaning
CHO Chinese hamster ovary cell
DMEM Dulbecco’s modified Eagle’s medium
ERT Enzyme replacement therapy
ELISA Enzyme-linked immunosorbent assay
FBS Fetal bovine serum
FDA Food and Drug Administration
GBA1 Glucocerebrosidase, Glucosylceramidase beta 1
GCase Glucocerebrosidase, Glucosylceramidase beta 1
GD Gaucher disease
GlcCer Glucosylceramide
293_FT Human embryonic kidney 293 cells
HP Heterogeneous population
HS High stringency
ICGG International Collaborative Gaucher Group
L17 Lineage 17
LS Low stringency
LV Lentiviral vector
LTR Long terminal repeat
MOI Multiplicity of infection
MTX Methotrexate
4MU 4-methylumbiliferone
4MUG 4-methylumbiliferon-β-D-glucopyranoside
qPCR Real-time quantitative PCR
SUS Unified Health System (Sistema Único de Saúde)
TDC Sodium taurodeoxycholate hydrate