| AI | Artificial intelligence |
| ALL | Acute lymphoblastic leukemia |
| ASOs | Antisense Oligonucleotides |
| CAR-T | Chimeric antigen receptor-T |
| COVID-19 | Coronavirus disease 2019 |
| CPP | Cell penetrating peptides |
| CRISPR | Clustered regularly interspaced short palindromic repeats |
| DMD | Duchenne muscular dystrophy |
| DNA | Deoxy ribonucleic acid |
| EVs | Extracellular vesicles |
| HTS | High-throughput screening |
| HSC | Hematopoietic stem cell |
| LNPs | Lipid Nanoparticles |
| MOF | Metal–organic frameworks |
| mRNA | Messenger RNA |
| PBAEs | Poly(beta-amino esters) |
| PEI | Polyethylenimine |
| PLGA | Poly (lactic-co-glycolic acid) |
| RNA | Ribonucleic acid |
| SB | Sleeping Beauty |
| SiRNA | Small interfering RNA |
| SMA | Spinal muscular atrophy |