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. 2025 Aug 5;14(15):5515. doi: 10.3390/jcm14155515
AI Artificial intelligence
ALL Acute lymphoblastic leukemia
ASOs Antisense Oligonucleotides
CAR-T Chimeric antigen receptor-T
COVID-19 Coronavirus disease 2019
CPP Cell penetrating peptides
CRISPR Clustered regularly interspaced short palindromic repeats
DMD Duchenne muscular dystrophy
DNA Deoxy ribonucleic acid
EVs Extracellular vesicles
HTS High-throughput screening
HSC Hematopoietic stem cell
LNPs Lipid Nanoparticles
MOF Metal–organic frameworks
mRNA Messenger RNA
PBAEs Poly(beta-amino esters)
PEI Polyethylenimine
PLGA Poly (lactic-co-glycolic acid)
RNA Ribonucleic acid
SB Sleeping Beauty
SiRNA Small interfering RNA
SMA Spinal muscular atrophy