TABLE 1.
Baseline Characteristics of the Study Population
| Placebo (n=7) | Ezetimibe 10 mg/d (n=30) | |
|---|---|---|
| Age, y | ||
| Mean | 37.6 | 37.0 |
| Range | 13–57 | 9–72 |
| Age subgroup, n (%) | ||
| <18 y | 1 (14) | 4 (13) |
| ≥18 y | 6 (86) | 26 (87) |
| Gender, n (%) | ||
| Female | 6 (86) | 18 (60) |
| Male | 1 (14) | 12 (40) |
| Race, n (%) | ||
| White | 6 (86) | 27 (90) |
| Asian | 0 (0) | 1 (3) |
| Hispanic | 1 (14) | 2 (7) |
| Body weight, kg | ||
| Mean | 63.0 | 67.5 |
| Range | 38.9–90.5 | 37.2–103.6 |
| Time since diagnosis, y | ||
| Mean | 15.4 | 15.0 |
| Range | 6–32 | 0–32 |
| Prior treatment of sitosterolemia, n (%) | ||
| None | 0 (0) | 10 (33) |
| Statins | 2 (29) | 8 (27) |
| Bile salt-binding resins | 4 (57) | 11 (37) |
| Ileal bypass surgery | 2 (29) | 3 (10) |
| Apheresis | 0 (0) | 1 (3) |