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. 2025 Sep 1;26(17):8497. doi: 10.3390/ijms26178497
AAV Adeno-Associated Virus
ABE Adenosine Base Editor
ALDP Adenoleukodistrophy Protein
APC Antigen-Presenting Cells
APOBEC Apolipoprotein B MRNA Editing Enzyme
ASCT Alanine, Serine, Cysteine Transporter
ATMP Advanced Therapy Medicinal Product
Att DNA Attachment Site
B2M Β-2 Microglobulin
BaEv Baboon Endogenous Virus
BPIFC Bpi Fold-Containing Family C
CA Capsid
CALD Cerebral Adrenoleukodystrophy
CAR Chimeric Antigen Receptor
CBE Cytosine Base Editor
CDMO Contract Development And Manufacturing Organization
CRISPR Clustered Regularly Interspaced Short Palindromic Repeats
CTE Constitutive Transport Element
DARPins Designed Ankyrin Repeat Proteins
DC Dendritic Cells
DDR DNA Damage Responses
DIS Dimerization Initiation Site
DMV Dolphin Morbillivirus
DSB Double-Strand Break
DSP Downstream Processing
GaLV Gibbon Ape Leukemia Virus
GBP3 Guanylate-Binding Protein 3
GMP Good Manufacturing Practices
GOI Gene Of Interest
HDR Homology-Directed Repair
HIV-1 Human Immunodeficiency Virus Type 1
HPV Human Papillomavirus
HSC Hematopoietic Stem Cell
HSPC Hematopoietic Stem And Progenitor Cell
IDLV Integrase Deficient Lentiviral Vector
IN Integrase
IRES Internal Ribosome Entry Site
ITR Inverted Terminal Repeat
LDAH Lipid Droplet-Associated Hydrolase
LDLR Low-Density Lipoprotein Receptor
LNP Lipid Nanoparticle
LTR Long Terminal Repeats
LVNP Lentivirus-Derived Nanoparticles
LVV Lentiviral Vectors
MA Matrix Protein
MHC-1 Major Histocompatibility Complexes Class 1
MLD Metachromatic Leukodystrophy
MPMV Mason-Pfizer Monkey Virus
MSD Major Splicing Donor
MV-H Measles Virus Hemagglutinin Protein
NC Nucleocapsid
Nef Negative Factor
NHEJ Non-Homologous End Joining
NHLRC1 NHL Repeat-Containing E3 Ubiquitin Protein Ligase 1
NPC Nuclear Pore Complexes
OAS1 2′-5′-Oligoadenylate Synthetase 1
ORF Open Reading Frame
ORI Origin Of Replication
PBS Primer Binding Site
PH Pleckstrin Homology
PIC Preintegration Complex
PKR Protein Kinase RNA-Activated
PPT Polypurine Tract
PR Protease
RCL Replication Competent Lentivirus
RD114 Feline Endogenous Retrovirus
Rev Regulator Of Expression Of Virion Proteins
RF Restriction Factor
RRE Rev Responsive Element
RT Reverse Transcriptase
RTE RNA Transport Element
RV Rabies Virus
S/MAR Scaffold/Matrix Associated Region
SA Splicing Acceptor
scFv Single-Chain Variable Fragments
SD Splicing Donor
SIN-LVV Self-Inactivating Lentiviral Vectors
SPM Secondary Primary Malignancies
SRV-1 Simian Retrovirus Type 1
SU Surface Glycoprotein
TAA Tumor-Associated Antigens
TALEN Transcription Activator-Like Effector Nucleases
TAR Transactivation-Reponse Element
Tat Trans-Activator Of Transcription
TM Transmembrane Glycoprotein
TRAP Tryptophan RNA-Binding Attenuation Protein
USP Upstream Processing
VHH Variable Heavy Domain Of Heavy Chain
Vif Virion Infectivity Factor
Vpr Viral Protein R
Vpu Vira Protein U
VSV-G Vesicular Stomatitis Virus Glycoprotein
WHX Woodchuck Hepatitis Virus X Protein
WPRE Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element
ZFN Zinc Finger Nuclease
ZNF425 Zinc Finger Protein 425