| AAV | Adeno-associated virus |
| ALS | Amyotrophic lateral sclerosis |
| BCA | Bicinchoninic Acid |
| C9orf72 | Chromosome 9 open reading frame 72 |
| CFPSA | Cell-free protein synthesis and assembly |
| DPR | Dipeptide repeat |
| eDRAC | Energy-dependent Drug Resin Affinity Chromatography |
| FTD | Frontotemporal dementia |
| G4C2 | GGGGCC |
| IHC | Immunohistochemistry |
| IP | Intraperitoneal |
| MSD | Meso Scale Discovery |
| P0 | Postnatal day 0 |
| PBMC | Peripheral blood mononuclear cell |
| PDI | Protein disulfide isomerase |
| PK | pharmacokinetic |
| pTDP-43 | Phosphorylated TAR DNA-binding protein 43 |
| SOD1 | Superoxide dismutase 1 |
| TBSE | Tris-Buffered Saline with EDTA |
| THIQ | Tetrahydroisoquinolone |