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. 2025 Dec 17;14(24):2012. doi: 10.3390/cells14242012
AAV Adeno-associated virus
ALS Amyotrophic lateral sclerosis
BCA Bicinchoninic Acid
C9orf72 Chromosome 9 open reading frame 72
CFPSA Cell-free protein synthesis and assembly
DPR Dipeptide repeat
eDRAC Energy-dependent Drug Resin Affinity Chromatography
FTD Frontotemporal dementia
G4C2 GGGGCC
IHC Immunohistochemistry
IP Intraperitoneal
MSD Meso Scale Discovery
P0 Postnatal day 0
PBMC Peripheral blood mononuclear cell
PDI Protein disulfide isomerase
PK pharmacokinetic
pTDP-43 Phosphorylated TAR DNA-binding protein 43
SOD1 Superoxide dismutase 1
TBSE Tris-Buffered Saline with EDTA
THIQ Tetrahydroisoquinolone