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. 2026 Jan 6;15:1691518. doi: 10.3389/fonc.2025.1691518

Table 2.

Ocular adverse events associated with select tyrosine kinase inhibitors (TKIs) and other small molecule inhibitors.

TKI/Small molecule inhibitor PMT Cancer indication Adverse ocular events
Imatinib BCR-ABL, cKIT, PDGFR CML, GIST, ALL Periorbital edema, conjunctival hemorrhage, blurred vision, dry eye, macular edema, optic disc edema (6, 34)
Dasatinib BCR-ABL, SRC CML, ALL Periorbital edema, macular edema, optic disc edema (6, 34)
Nilotinib BCR-ABL CML Periorbital edema, eyelid redness, chorioretinopathy, visual disturbances (6, 34).
Ponatinib BCR-ABL, VEGFR, FGFR CML Retinal vein occlusion, macular edema, retinal hemorrhage, optic disc edema (15, 35)
Ibrutinib BTK CLL, MCL Blurred vision, dry eye, uveitis, cystoid macular edema, ocular bleeding (34)
Ruxolitinib JAK1/2 Myelofibrosis, PV Herpes zoster ophthalmicus with keratitis and uveitis (19)
Dabrafenib BRAF Melanoma Uveitis, cystoid macular edema, uveal effusion, serous/exudative retinal detachment (36)
Vemurafenib BRAF Melanoma Uveitis, conjunctivitis, dry eye, VKH-like syndrome (37)
Midostaurin FLT3 AML Eyelid edema (~3%); rare blurred vision or photophobia; no consistent structural ocular signal in AML trials (20).
Gilteritinib FLT3 AML Visual changes reported at low rates, including blurred vision, dry eye disease, and retinal hemorrhage (~6–7% each); rare differentiation syndrome which can include visual symptoms (21).
Erdafitinib FGFR1–4 Metastatic urothelial carcinoma Central serous retinopathy, RPED, dry eye, PUK (38)
Crizotinib ALK, ROS1 NSCLC Photopsia, blurred vision, vitreous floaters (39)
Venetoclax BCL2 inhibitor CLL, AML Blurred vision (transient, non-pathologic) (40)

Representative agents are listed with their primary molecular targets (PMT), approved cancer indications, and characteristic ocular toxicities. Reported events span benign, common findings (for example, periorbital edema with BCR-ABL inhibitors) to vision-threatening complications (for example, retinal vein occlusion with ponatinib, uveitis/CME with ibrutinib). Incidence and severity vary by agent and mechanism of action. Agents used outside hematologic malignancies (for example, BRAF or ALK/ROS1 inhibitors) are included where they illustrate class-specific ocular signals relevant to oncology practice.