MPS IVA	Mucopolysaccharidosis IVA
GALNS	N-acetylgalactosamine-6-sulfate sulfatase
GAGs	Glycosaminoglycans
KS	Keratan sulfate
C6S	Chondroitin-6-sulfate
LV	Lentiviral vectors
LVGT	Lentiviral gene therapy
VSVG	Vesicular stomatitis virus glycoprotein
IV	Intravenous
IA	Intraarticular
ERT	Enzyme replacement therapy
AAV	Adeno-associated virus
ECM	Extracellular matrix
HE	Hematoxylin and eosin
VCN	Vector copy number
LDL	Low-density lipoprotein
KO	Knockout
WBCs	White blood cells
BMCs	Bone marrow cells
LC-MS/MS	Liquid chromatography–tandem mass spectrometry
ddPCR	Digital droplet polymerase chain reaction
qPCR	Quantitative polymerase chain reaction
ALT	Alanine aminotransferase
AST	Aspartate aminotransferase
ELISA	Enzyme-linked immunosorbent assay
WT	Wild-type
UT	Untreated
IHC	Immunohistochemistry
μCT	Micro-computational tomography