| HTA | Health Technology Assessment |
| SHEER | Spillovers in Health Economic Evaluation and Research |
| SMA | Spinal Muscular Atrophy |
| NICE | United Kingdom’s National Institute of Health and Care Excellence |
| CADTH | Canada’s Drug and Health Technology Agency |
| NHI | National Health Institute |
| SBU | Swedish Agency for Health Technology Assessment |
| HAS | Haute Autorité de Santé |
| HRQoL | Health-Related Quality of Life |
| CUA | Cost–Utility Analysis |
| UK | United Kingdom |
| MFA | Multiple Factor Analysis |
| PAM | Partitioning Around Medoids |
| ICER | Institute for Clinical and Economic Review |
| iPCQ | iMTA Productivity Cost Questionnaire |
| SF-HLQ | Short Form-Health and Labour Questionnaire |
| HCM | Human Capital Method |
| HLQ | Health and Labour Questionnaire |
| USA | United States of America |
| PRODISQ | PROductivity and DISease Questionnaire |