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. 2026 Feb 2;14(2):344. doi: 10.3390/biomedicines14020344
AAV adeno-associated virus
APCs antigen-presenting cells
BCAAs branched-chain amino acids
CAV3 caveolin 3
CMC cardiomyocyte
CPT1 carnitine palmitoyltransferase 1
CUPID 1 Calcium Up-Regulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (Phase 1/2)
CUPID 2 Calcium Up-Regulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (Phase 2b)
FAO fatty acid oxidation
HF heart failure
HFpEF heart failure with preserved ejection fraction
HFrEF heart failure with reduced ejection fraction
IFM interfibrillar mitochondria
LR laminin receptor
LVNC left ventricular non-compaction cardiomyopathy
MCARD molecular cardiac surgery with recirculating delivery
MHC major histocompatibility complex
mPTP mitochondrial permeability transition pore
nAbs neutralizing antibodies
NOS nitric oxide synthase
PGC-1α coactivator peroxisome-proliferator γ coactivator 1 α
PNM perinuclear mitochondria
PPARα peroxisome proliferator-activated receptor α (PPARα)
rAAV recombinant AAV adeno-associated virus
SSM sarcoplasmic submembrane mitochondria