| CAIR ATIC |
5-aminoimidazole-4-carboxylate ribonucleotide 5-Aminoimidazole-4-carboxamide ribonucleotide formyltransferase |
| PPAT | Amidophosphoribosyltransferase |
| ADA | Adenosine Deaminase |
| ADK | Adenosine Kinase |
| ADSL | Adenylosuccinate Lyase |
| ALS | Amyotrophic Lateral Sclerosis |
| C9orf72 CHX |
Chromosome 9, Open Reading Frame 72 Cycloheximide |
| DNPB | De novo purine biosynthesis |
| DPR | Dipeptide Repeat Protein |
| CD73 | Ecto-5′-nucleotidase |
| EV EAAT2 |
Empty Vector Excitatory amino acid transporter 2 |
| FGAMS | Formylglycinamide ribonucleotide amidotransferase |
| poly-GA | Glycine-Alanine |
| poly-GR | Glycine-Arginine |
| poly-GP | Glycine-Proline |
| HRE | Hexanucleotide Repeat Expansion |
| HGPRT | Hypoxanthine-Guanine Phosphoribosyltransferase |
| iNPC | Induced Neural Progenitor Cell |
| iAstrocyte | Induced Neural Progenitor Cell-Derived Astrocyte |
| IMP | Inosine Monophosphate |
| LLPS LV-ADA LV-EV NV |
Liquid−Liquid Phase Separation lentivirus expressing ADA lentivirus expressing empty vector non-virally treated |
| PAICS | Phosphoribosylaminoimidazole carboxylase/phosphoribosylaminoimidazole succinocarboxamide synthetase |
| GART | Phosphoribosylglycinamide formyltransferase/phosphoribosylglycinamide synthetase/phosphoribosylaminoimidazole synthetase |
| poly-PA | Proline-Alanine |
| poly-PR | Proline-Arginine |
| PNP | Purine Nucleoside Phosphorylase |
| SCID SRSF1 SAICAR RuvBL2 |
Severe Combined Immunodeficiency Serine/arginine-rich splicing factor 1 succinylaminoimidazole carboxamide ribonucleotide RuvB-like 2 |
| XO | Xanthine Oxidase |