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. 2026 Feb 21;18(2):265. doi: 10.3390/pharmaceutics18020265
siRNA small interfering RNA
CD cyclodextrin
NVs nanovectors
RNAi RNA interference
miRNA microRNA
LNPs lipid nanoparticles
hATTR hereditary transthyretin amyloidosis
BBB blood–brain barrier
cCD cationic cyclodextrin
AML acute myeloid leukemia
TAMs tumor-associated macrophages