| ABX | Ambroxol |
| AE | Adverse events |
| ER | Endoplasmic reticulum |
| ERT | Enzyme replacement therapy |
| GBA1 | Gene encoding glucocerebrosidase |
| GBA-PD | Parkinson’s disease associated with GBA variants |
| GD | Gaucher disease |
| GD3 | Type III Gaucher disease |
| GD1-PD | Type I Gaucher disease with increased risk of Parkinson’s disease |
| INR | International normalized ratio |
| Lyso-Gb1/Lyso-GL1 | Glucosylsphingosine |
| nGD | Neuronopathic Gaucher disease |
| PCT | Pharmacological chaperone therapy |
| PD | Parkinson’s disease |
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