Table 1.
Gender | Year of enrolment | Natural history protocol (number of subjects) | Enzyme replacement protocol (number of subjects) |
---|---|---|---|
Male | 1996 | 1 | 1 |
1997 | 1 | 0 | |
1998 | 2 | 1 | |
1999 | 2 | 19 | |
2000 | 18 | 6 | |
2001 | 5 | 4 | |
2002 | 9 | 4 | |
2003 | 11 | 1 | |
Total | 49 | 36 | |
Female | 1999 | 1 | — |
2000 | 6 | — | |
2001 | 9 | — | |
2002 | 6 | — | |
2003 | 2 | — | |
Total | 24 | — |