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. 2009 Jan 22;100(2):266–273. doi: 10.1038/sj.bjc.6604867

Table 3. Best overall response in first-line treatment according to MMR status.

Patients evaluable for response pMMR (n=453) dMMR MLH1-hypermethylation (n=12) dMMR total (n=16) P-value# pMMR vs dMMR hypermethylation P-value# pMMR vs dMMR total
Best overall response
 Complete response 16 (4%)    
 Partial response 123 (27%) 4 (33%) 4 (25%)    
 Stable disease 235 (52%) 3 (25%) 5 (31%)    
 Progressive disease 79 (17%) 5 (42%) 7 (44%)    
           
Response rate (95% CI) 31% (27–35%) 33% (10–65%) 25% (7–52%) 0.84 0.63
  n=139 n=4 n=4    
Disease control (95% CI) 83% (79–86%) 58% (28–85%) 56% (30–80%) 0.031 0.008
  n=374 n=7 n=9    
           
Sequential treatment n=239 n=5 n=8    
           
 Response rate (95% CI) 17% (13–23%) 40% (5–85%) 25% (3–65%) 0.19 0.57
  n=41 n=2 n=2    
 Disease control (95% CI) 76% (70–81%) 60% (15–95%) 50% (16–84%) 0.40 0.09
  n=182 n=3 n=4    
           
Combination treatment n=214 n=7 n=8    
           
 Response rate (95% CI) 46% (39–53%) 29% (4–71%) 25% (3–65%) 0.46 0.30
  n=98 n=1 n=2    
 Disease control (95% CI) 90% (85–93%) 57% (18–90%) 63% (25–92%) 0.033 0.048
  n=193 n=4 n=5    

#P-value χ2.