Table 1.
IDS Activity (nmol/4 h/mg) |
||||
---|---|---|---|---|
T1 | T6 | T12 | T18 | |
WT | 320 ± 27 | 243 ± 32.1 | 220 ± 36.2 | 198 ± 18.9 |
Idsy/− | 27 ± 1.5 | 24 ± 0.6 | 18 ± 1.1 | |
Idsy/−+IDS | 2400 | |||
Idsy/−+IDS | 2700 | |||
Idsy/−+IDS | 1995 | |||
Idsy/−+IDS | 2090 | |||
Idsy/−+IDS | 2405 | |||
Idsy/−+IDS | 2820 | |||
Idsy/−+IDS | 1900 | |||
Idsy/−+IDS | 2340 | |||
Idsy/−+IDS | 2300 | 1410 | 909 | 820 |
Idsy/−+IDS | 1900 | 950 | 659 | 420 |
Idsy/−+IDS | 2435 | 1680 | 1409 | 1219 |
Idsy/−+IDS | 2230 | 1735 | 1380 | 1022 |
IDS activity in the plasma measured at different times after therapy (T1, T6, T12, and T18: 1, 6, 12, and 18 months after the injection, respectively) of WT (n = 3), Idsy/− (n = 3), and AAV2/5CMV-hIDS-injected Idsy/− mice.