Table 1. Clinical presentation and identified mutations.
WD NO | Sex | Vital status | Age at onset (year) | Age at diagnosis (year) | Diagnostic Delay (months) | Year of diagnosis | Country of origin | Variant 1 | Variant 2 |
---|---|---|---|---|---|---|---|---|---|
FHF | |||||||||
15 | M | Alive | 30 | 30 | 0.2 | 1993 | Denmark | p.H1069Q | p.G1158V |
20-S | M | Dead (FHF) | 13 | 13 | NA | <1966 | Denmark | p.I1021K | p.T1220M |
25 | F | Alive | 21 | 21 | 0.2 | 1991 | Denmark | p.W779X | p.H1069Q |
25-S | F | Dead (FHF) | 16 | 16 | 0.2 | 1990 | Denmark | p.W779X | p.H1069Q |
34 | M | Alive-TX | 12 | 12 | 0.2 | 1994 | Denmark | p.W779X | p.M769V |
43 | M | Alive-TX | 12 | 12 | 0.2 | 2005 | Denmark | p.W779X | p.T977M |
41 | F | Alive-TX | 23 | 23 | 0.5 | 2007 | Iceland | c.2007_2013delATATGCT | c2007_2013delATATGCT, |
44 | M | Dead (FHF) | 9 | 9 | NA | 1974 | Denmark | p.G1266R | c.1708-?_1946+?del |
B | M | Alive-TX | 11 | 11 | 0.2 | 1994 | Denmark | NA | NA |
F-S1 | F | Dead (FHF) | 13 | 13 | 0.2 | 1978 | Denmark | NA | NA |
Hepatitis+Hemolysis | |||||||||
9a | M | Alive | 11 | 11 | 4 | 1981 | Turkey | c.4022-?_4398+?del | c.4022-?_4398+?del |
20 | M | Alive | 8 | 11 | 36 | 1966 | Denmark | p.I1021K | T1220M |
24 | F | Alive | 33 | 34 | 8 | 2001 | Iceland | c2007_2013delATATGCT | c2007_2013delATATGCT |
31 | M | Alive | 11 | 11 | 2 | 2003 | Denmark | p.W779X | G943D |
37 | F | Alive | 14 | 16 | 24 | 2004 | Denmark | p.W779X | G1266R |
42 | F | Alive | 15 | 15 | 6 | 1992 | Denmark | p.H1069Q | G1266R |
45 | M | Alive | 16 | 16 | 6 | 2000 | Denmark | p.P1273 L | c.2304insC |
CLD | |||||||||
F | F | Alive | 17 | 17 | NA | 1969 | Denmark | NA | NA |
10 | M | Alive | 13 | 14 | 13 | 1994 | Pakistan | p.L1304F | p.L1304F |
11 | F | Alive | 39 | 39 | 2 | 1989 | Denmark | p.R1041W | p.T1220M |
19 | M | Alive-TX | 39 | 39 | NA | 1990 | Israel | p.D642H | p.D642H |
22 | F | Alive | 13 | 13 | 6 | 1969 | Denmark | p.G943D | p.S1363F |
32 | M | Alive | 7 | 7 | 3 | 2004 | Denmark | p.H1069Q | p.P1273 L |
38 | M | Alive | 13 | 13 | 6 | 1995 | Denmark | p.H1069Q | p.S1363F |
39 | F | Alive | 9 | 10 | 14 | 2007 | Denmark | p.I1021K | p.H1069Q |
40 | M | Alive | 7 | 7 | 2 | 2007 | Denmark | p.H1069Q | p.H1069Q |
17 | M | Dead (CLD) | 30 | 32 | 21 | 1995 | Denmark | p.M769V | p.G943D |
C | M | Alive-TX | 33 | 34 | 14 | 1989 | Denmark | NA | NA |
Neurological symptoms | |||||||||
6 | M | Alive | 12 | 12 | 0 | 1969 | Denmark | p.W779X | p.W779X |
13 | F | Alive | 23 | 33 | 120 | 1978 | Denmark | p.T1220M | p.Q1351X |
14 | M | Alive | 26 | 26 | 4 | 1979 | Denmark | p.P1273 L | c.4022-2A>G |
16 | M | Alive | 14 | 14 | 1 | 1995 | Turkey | p.N1270S | p.N1270S |
21 | F | Alive | 17 | 18 | 13 | 1987 | Denmark | p.H1069Q | p.S1363F |
23 | F | Alive | 38 | 38 | 5 | 1997 | Denmark | p.W779X | p.R1041W |
26 | M | Alive | 34 | 35 | 7 | 1988 | Denmark | p.H1069Q | p.A1003T |
27 | F | Alive | 10 | 17 | 84 | 1993 | Denmark | p.H1069Q | p.S1363F |
29 | F | Alive-TX | 14 | 19 | 60 | 1994 | Turkey | p.H1069Q | p.G1341D |
33 | F | Alive | 23 | 24 | 14 | 2004 | Turkey | p.M1169T | p.M1169T |
35 | M | Alive | 17 | 17 | 6 | 2004 | Korea | p.R778 L | p.R778 L |
36 | M | Alive | 28 | 30 | 27 | 2004 | Serbia | p.G591D | p.R616Q |
2 | M | Alive | 19 | 19 | NA | 1978 | Denmark | p.T1220M | p.G1266R |
6-S | M | Alive | NA | 15 | NA | 1968 | Denmark | p.W779X | p.W779X |
A | F | Dead-TX (HCC) | 27 | 30 | 37 | 1984 | Denmark | NA | NA |
D | F | Alive | 23 | 29 | 72 | 1996 | NA | NA | |
E | F | Dead (Other) | 20 | 20 | NA | 1959 | NA | NA | |
Identified as asymptomatic siblings who started treatment before symptomatic disease | |||||||||
2-S | F | Dead (accident) | 17 | 17 | NA | 1978 | Denmark | p.T1220M | p.G1266R |
F-S2 | M | Dead (accident) | 20 | 20 | NA | NA | Denmark | NA | NA |
F-S3 | F | Alive | 10 | 10 | 36 | 1975 | Denmark | NA | NA |
27-S | M | Alive | 15 | 15 | 0 | 2000 | Denmark | p.H1069Q | p.S1363F |
Abbreviations: CLD, chronic liver disease; FHF, fulminant hepatic failure; HCC, hepatocellular carcinoma; NA, Not available; TX, liver transplantation
Patients belonging to the same family have the same number or letter. ‘S' denotes sibling to the first patient diagnosed in the particular family.